In utero gene editing for monogenic lung disease.
Sci Transl Med.
2019 Apr 17;11(488). doi: 10.1126/scitranslmed.aav8375. PubMed PMID:
30996081; PubMed Central PMCID:
PMC6822403.
In utero CRISPR-mediated therapeutic editing of metabolic genes.
Nat Med.
2018 Oct;24(10):1513-1518. doi: 10.1038/s41591-018-0184-6. Epub 2018 Oct 8. PubMed PMID:
30297903; PubMed Central PMCID:
PMC6249685.
Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells.
Nucleic Acids Res.
2018 Sep 19;46(16):8275-8298. doi: 10.1093/nar/gky548. PubMed PMID:
29947794; PubMed Central PMCID:
PMC6144820.
Efficient In Vivo Liver-Directed Gene Editing Using CRISPR/Cas9.
Mol Ther.
2018 May 2;26(5):1241-1254. doi: 10.1016/j.ymthe.2018.02.023. Epub 2018 Mar 6. PubMed PMID:
29599079; PubMed Central PMCID:
PMC5993986.
Combined targeting of EGFR/HER promotes anti-tumor efficacy in subsets of KRAS mutant lung cancer resistant to single EGFR blockade.
Oncotarget.
2015 Aug 21;6(24):20132-44. doi: 10.18632/oncotarget.3853. PubMed PMID:
25992771; PubMed Central PMCID:
PMC4652993.
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