Quality of life in a large multinational haemophilia B cohort (The B-Natural study) - Unmet needs remain.
Berntorp E, LeBeau P, Ragni MV, Borhany M, Abajas YL, Tarantino MD, Holstein K, Croteau SE, Liesner R, Tarango C, Carvalho M, McGuinn C, Funding E, Kempton CL, Bidlingmaier C, Cohen A, Oldenburg J, Kearney S, Knoll C, Kuriakose P, Acharya S, Reiss UM, Kulkarni R, Witkop M, Lethagen S, Krouse R, Shapiro AD, Astermark J.
Berntorp E, et al.
Haemophilia. 2022 May;28(3):453-461. doi: 10.1111/hae.14525. Epub 2022 Mar 8.
Haemophilia. 2022.
PMID: 35263495
Free PMC article.
Twenty-nine participants had inhibitors or a history of inhibitors. Three versions of the EQ-5D instrument were used as a measure of QoL: proxy (ages 4-7), youth (ages 8-15) and self (age 16+). ...The majority of the mild and moderate severe participants reported a normal …
Twenty-nine participants had inhibitors or a history of inhibitors. Three versions of the EQ-5D instrument were used as a measure of …