Format
Sort by
Items per page

Send to

Choose Destination

Best matches for "gene therapy":

Gene therapy for neurological disorders. Choong CJ et al. Expert Opin Biol Ther. (2016)

Adeno-Associated Virus (AAV) gene therapy for cystic fibrosis: current barriers and recent developments. Guggino WB et al. Expert Opin Biol Ther. (2017)

State-of-the-art human gene therapy: part I. Gene delivery technologies. Wang D et al. Discov Med. (2014)

Search results

Items: 1 to 20 of 54224

1.

Artificial MicroRNAs Targeting C9orf72 Can Reduce Accumulation of Intra-nuclear Transcripts in ALS and FTD Patients.

Martier R, Liefhebber JM, Miniarikova J, van der Zon T, Snapper J, Kolder I, Petry H, van Deventer SJ, Evers MM, Konstantinova P.

Mol Ther Nucleic Acids. 2019 Jan 30;14:593-608. doi: 10.1016/j.omtn.2019.01.010. [Epub ahead of print]

PMID:
30776581
2.

Exosome-mediated horizontal gene transfer occurs in double-strand break repair during genome editing.

Ono R, Yasuhiko Y, Aisaki KI, Kitajima S, Kanno J, Hirabayashi Y.

Commun Biol. 2019 Feb 8;2:57. doi: 10.1038/s42003-019-0300-2. eCollection 2019.

PMID:
30775458
3.

Transcriptional Targeting and MicroRNA Regulation of Lentiviral Vectors.

Merlin S, Follenzi A.

Mol Ther Methods Clin Dev. 2019 Jan 8;12:223-232. doi: 10.1016/j.omtm.2018.12.013. eCollection 2019 Mar 15. Review.

PMID:
30775404
4.

Data collection infrastructure for patient outcomes in the UK - opportunities and challenges for cell and gene therapies launching.

Jørgensen J, Mungapen L, Kefalas P.

J Mark Access Health Policy. 2019 Feb 4;7(1):1573164. doi: 10.1080/20016689.2019.1573164. eCollection 2019.

PMID:
30774785
5.

New therapies for the treatment of heart failure: a summary of recent accomplishments.

Machaj F, Dembowska E, Rosik J, Szostak B, Mazurek-Mochol M, Pawlik A.

Ther Clin Risk Manag. 2019 Jan 22;15:147-155. doi: 10.2147/TCRM.S179302. eCollection 2019. Review.

PMID:
30774351
6.

Production, Purification, and Quality Control for Adeno-associated Virus-based Vectors.

Fripont S, Marneffe C, Marino M, Rincon MY, Holt MG.

J Vis Exp. 2019 Jan 29;(143). doi: 10.3791/58960.

PMID:
30774140
7.

Lentiviral Gene Therapy For Bone Repair Using Human Umbilical Cord Blood Derived-Mesenchymal Stem Cells.

Bougioukli S, Saitta B, Sugiyama O, Tang A, Elphingstone J, Evseenko D, Lieberman JR.

Hum Gene Ther. 2019 Feb 16. doi: 10.1089/hum.2018.054. [Epub ahead of print]

PMID:
30773946
8.

Two Decades of Molecular Therapy and a 35-Year Personal View of Changes in Gene Therapy.

Williams DA.

Mol Ther. 2019 Feb 14. pii: S1525-0016(19)30044-9. doi: 10.1016/j.ymthe.2019.02.003. [Epub ahead of print] No abstract available.

PMID:
30773447
9.

Hematopoietic stem cell transplantation for mucopolysaccharidoses; past, present, and future.

Taylor M, Khan S, Stapleton M, Wang J, Chen J, Wynn R, Yabe H, Chinen Y, Boelens JJ, Mason RW, Kubaski F, Horovitz DDG, Barth AL, Serafini M, Bernardo ME, Kobayashi H, Orii KE, Suzuki Y, Orii T, Tomatsu S.

Biol Blood Marrow Transplant. 2019 Feb 14. pii: S1083-8791(19)30137-5. doi: 10.1016/j.bbmt.2019.02.012. [Epub ahead of print] Review.

PMID:
30772512
10.

Therapeutics strategies against cancer stem cell in breast cancer.

Ghasemi F, Sarabi PZ, Athari SS, Esmaielzadeha A.

Int J Biochem Cell Biol. 2019 Feb 14. pii: S1357-2725(19)30022-6. doi: 10.1016/j.biocel.2019.01.015. [Epub ahead of print]

PMID:
30772480
11.

Protease-Activatable Adeno-Associated Virus Vector for Gene Delivery to Damaged Heart Tissue.

Guenther CM, Brun MJ, Bennett AD, Ho ML, Chen W, Zhu B, Lam M, Yamagami M, Kwon S, Bhattacharya N, Sousa D, Evans AC, Voss J, Sevick-Muraca EM, Agbandje-McKenna M, Suh J.

Mol Ther. 2019 Jan 29. pii: S1525-0016(19)30034-6. doi: 10.1016/j.ymthe.2019.01.015. [Epub ahead of print]

PMID:
30772143
12.

Development of a novel frameless skull-mounted ball-joint guide array for use in image-guided neurosurgery.

Sudhakar V, Mahmoodi A, Bringas JR, Naidoo J, Kells A, Samaranch L, Fiandaca MS, Bankiewicz KS.

J Neurosurg. 2019 Feb 15:1-10. doi: 10.3171/2018.10.JNS182169. [Epub ahead of print]

PMID:
30771782
13.

Long-term correction of hemophilia B using adenoviral delivery of CRISPR/Cas9.

Stephens CJ, Lauron EJ, Kashentseva E, Lu ZH, Yokoyama WM, Curiel DT.

J Control Release. 2019 Feb 13. pii: S0168-3659(19)30082-3. doi: 10.1016/j.jconrel.2019.02.009. [Epub ahead of print]

PMID:
30771412
14.

A combined immunodeficiency with severe infections, inflammation and allergy caused by ARPC1B deficiency.

Volpi S, Cicalese MP, Tuijnenburg P, Tool ATJ, Cuadrado E, Ahanchian H, Alzyoud R, Akdemir ZC, Barzaghi F, Blank A, Boisson B, Bottino C, Caorsi R, Casanova JL, Chiesa S, Chinn IK, Dückers G, Enders A, Erichsen HC, Forbes LR, Gambin T, Gattorno M, Karimiani EG, Giliani S, Gold MS, Abu-Halaweh M, Brigida I, Jacobsen EM, Jansen MH, King JR, Laxer RM, Lupski JR, Mace E, Marcenaro S, Maroofian R, Meijer AB, Niehues T, Notarangelo LD, Orange J, Pannicke U, Pearson C, Picco P, Quinn PJ, Schulz A, Seeborg F, Stray-Pedersen A, Tawamie H, van Leeuwen EMM, Aiuti A, Yeung R, Schwarz K, Kuijpers TW.

J Allergy Clin Immunol. 2019 Feb 13. pii: S0091-6749(19)30206-4. doi: 10.1016/j.jaci.2019.02.003. [Epub ahead of print]

PMID:
30771411
15.

Chitosan nanopolymers: An overview of drug delivery against cancer.

Shanmuganathan R, Edison TNJI, LewisOscar F, Ponnuchamy K, Shanmugam S, Pugazhendhi A.

Int J Biol Macromol. 2019 Feb 13. pii: S0141-8130(18)37203-9. doi: 10.1016/j.ijbiomac.2019.02.060. [Epub ahead of print] Review.

PMID:
30771392
16.
17.

Regulatable adenovector harboring the GFP and Yamanaka genes for implementing regenerative medicine in the brain.

Lehmann M, Canatelli-Mallat M, Chiavellini P, Morel GR, Reggiani PC, Hereñú CB, Goya RG.

Gene Ther. 2019 Feb 15. doi: 10.1038/s41434-019-0063-x. [Epub ahead of print]

PMID:
30770896
18.

scFv6.C4 DNA vaccine with fragment C of Tetanus toxin increases protective immunity against CEA-expressing tumor.

Zanetti BF, Ferreira CP, de Vasconcelos JRC, Han SW.

Gene Ther. 2019 Feb 15. doi: 10.1038/s41434-019-0062-y. [Epub ahead of print]

PMID:
30770895
19.

PLOD3 suppression exerts an anti-tumor effect on human lung cancer cells by modulating the PKC-delta signaling pathway.

Baek JH, Yun HS, Kwon GT, Lee J, Kim JY, Jo Y, Cho JM, Lee CW, Song JY, Ahn J, Kim JS, Kim EH, Hwang SG.

Cell Death Dis. 2019 Feb 15;10(3):156. doi: 10.1038/s41419-019-1405-8.

PMID:
30770789
20.

Considerations for the use of Cre recombinase for conditional gene deletion in the mouse lens.

Lam PT, Padula SL, Hoang TV, Poth JE, Liu L, Liang C, LeFever AS, Wallace LM, Ashery-Padan R, Riggs PK, Shields JE, Shaham O, Rowan S, Brown NL, Glaser T, Robinson ML.

Hum Genomics. 2019 Feb 15;13(1):10. doi: 10.1186/s40246-019-0192-8.

Supplemental Content

Loading ...
Support Center