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Items: 1 to 20 of 26

1.

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia.

Cavazzana-Calvo M, Payen E, Negre O, Wang G, Hehir K, Fusil F, Down J, Denaro M, Brady T, Westerman K, Cavallesco R, Gillet-Legrand B, Caccavelli L, Sgarra R, Maouche-Chrétien L, Bernaudin F, Girot R, Dorazio R, Mulder GJ, Polack A, Bank A, Soulier J, Larghero J, Kabbara N, Dalle B, Gourmel B, Socie G, Chrétien S, Cartier N, Aubourg P, Fischer A, Cornetta K, Galacteros F, Beuzard Y, Gluckman E, Bushman F, Hacein-Bey-Abina S, Leboulch P.

Nature. 2010 Sep 16;467(7313):318-22. doi: 10.1038/nature09328.

2.

Hemoglobin gene therapy for β-thalassemia.

Bank A.

Hematol Oncol Clin North Am. 2010 Dec;24(6):1187-201. doi: 10.1016/j.hoc.2010.08.002. Review.

PMID:
21075288
3.

Current status of globin gene therapy for the treatment of beta-thalassaemia.

Lisowski L, Sadelain M.

Br J Haematol. 2008 May;141(3):335-45. doi: 10.1111/j.1365-2141.2008.07098.x. Review.

PMID:
18410569
5.

Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.

Payen E, Leboulch P.

Hematology Am Soc Hematol Educ Program. 2012;2012:276-83. doi: 10.1182/asheducation-2012.1.276. Review.

PMID:
23233592
6.

Hematopoietic stem cell gene transfer for the treatment of hemoglobin disorders.

Persons DA.

Hematology Am Soc Hematol Educ Program. 2009:690-7. doi: 10.1182/asheducation-2009.1.690. Review.

PMID:
20008255
7.

Hematopoietic stem cell transplantation for people with ß-thalassaemia major.

Jagannath VA, Fedorowicz Z, Al Hajeri A, Sharma A.

Cochrane Database Syst Rev. 2016 Nov 30;11:CD008708. Review.

PMID:
27900772
8.

Haemoglobinopathies in southeast Asia.

Fucharoen S, Winichagoon P.

Indian J Med Res. 2011 Oct;134:498-506. Review.

9.
10.

Progress toward the genetic treatment of the beta-thalassemias.

Sadelain M, Lisowski L, Samakoglu S, Rivella S, May C, Riviere I.

Ann N Y Acad Sci. 2005;1054:78-91. Review.

PMID:
16339654
11.

Towards more successful gene therapy clinical trials for β-thalassemia.

Drakopoulou E, Papanikolaou E, Georgomanoli M, Anagnou NP.

Curr Mol Med. 2013 Sep;13(8):1314-30. Review.

PMID:
23865429
12.

[γ-Globin Inductive Therapy of β-thalassemia and Its Relationship with MicroRNA].

Li YY, Gu J, Yu DN.

Zhongguo Shi Yan Xue Ye Xue Za Zhi. 2016 Apr;24(2):627-31. doi: 10.7534/j.issn.1009-2137.2016.02.060. Review. Chinese.

PMID:
27151042
13.

Gene therapy for β-thalassaemia: the continuing challenge.

Yannaki E, Emery DW, Stamatoyannopoulos G.

Expert Rev Mol Med. 2010 Oct 1;12:e31. doi: 10.1017/S1462399410001626. Review.

PMID:
20883576
14.

Pathophysiology and therapy for haemoglobinopathies. Part II: thalassaemias.

Urbinati F, Madigan C, Malik P.

Expert Rev Mol Med. 2006 May 9;8(10):1-26. Review.

PMID:
16684395
15.

Hematopoietic stem cell transplantation for people with ß-thalassaemia major.

Jagannath VA, Fedorowicz Z, Al Hajeri A, Hu N, Sharma A.

Cochrane Database Syst Rev. 2011 Oct 5;(10):CD008708. doi: 10.1002/14651858.CD008708.pub2. Review. Update in: Cochrane Database Syst Rev. 2014;10:CD008708.

PMID:
21975785
16.

α-Globin as a molecular target in the treatment of β-thalassemia.

Mettananda S, Gibbons RJ, Higgs DR.

Blood. 2015 Jun 11;125(24):3694-701. doi: 10.1182/blood-2015-03-633594. Review.

17.

Gene therapy for hemoglobinopathies: the state of the field and the future.

Chandrakasan S, Malik P.

Hematol Oncol Clin North Am. 2014 Apr;28(2):199-216. doi: 10.1016/j.hoc.2013.12.003. Review.

18.

Recent trends for novel options in experimental biological therapy of β-thalassemia.

Finotti A, Gambari R.

Expert Opin Biol Ther. 2014 Oct;14(10):1443-54. doi: 10.1517/14712598.2014.927434. Review.

PMID:
24934764
19.

Alternative options for DNA-based experimental therapy of β-thalassemia.

Gambari R.

Expert Opin Biol Ther. 2012 Apr;12(4):443-62. doi: 10.1517/14712598.2012.665047. Review.

PMID:
22413823
20.

Studies in haemoglobin E beta-thalassaemia.

Olivieri NF, Muraca GM, O'Donnell A, Premawardhena A, Fisher C, Weatherall DJ.

Br J Haematol. 2008 May;141(3):388-97. doi: 10.1111/j.1365-2141.2008.07126.x. Review.

PMID:
18410572
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