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Items: 9

1.

Allele-specific silencing of mutant huntingtin and ataxin-3 genes by targeting expanded CAG repeats in mRNAs.

Hu J, Matsui M, Gagnon KT, Schwartz JC, Gabillet S, Arar K, Wu J, Bezprozvanny I, Corey DR.

Nat Biotechnol. 2009 May;27(5):478-84. doi: 10.1038/nbt.1539. Epub 2009 May 3.

2.

Personalized gene silencing therapeutics for Huntington disease.

Kay C, Skotte NH, Southwell AL, Hayden MR.

Clin Genet. 2014 Jul;86(1):29-36. doi: 10.1111/cge.12385. Epub 2014 Apr 11. Review.

PMID:
24646433
3.

Homozygous Machado Joseph Disease: a case report and review of literature.

Lysenko L, Grewal RP, Ma W, Peddareddygari LR.

Can J Neurol Sci. 2010 Jul;37(4):521-3. Review. No abstract available.

PMID:
20724264
4.

Oligonucleotide therapeutic approaches for Huntington disease.

Sah DW, Aronin N.

J Clin Invest. 2011 Feb;121(2):500-7. doi: 10.1172/JCI45130. Epub 2011 Feb 1. Review.

5.

[Gene silencing approaches for the treatment of Huntington's disease].

Merienne N, D├ęglon N.

Med Sci (Paris). 2015 Feb;31(2):159-67. doi: 10.1051/medsci/20153102012. Epub 2015 Mar 4. Review. French.

6.

Using non-coding small RNAs to develop therapies for Huntington's disease.

Zhang Y, Friedlander RM.

Gene Ther. 2011 Dec;18(12):1139-49. doi: 10.1038/gt.2011.170. Review.

PMID:
22158031
7.

Huntingtin-lowering strategies in Huntington's disease: antisense oligonucleotides, small RNAs, and gene editing.

Aronin N, DiFiglia M.

Mov Disord. 2014 Sep 15;29(11):1455-61. doi: 10.1002/mds.26020. Epub 2014 Aug 27. Review.

PMID:
25164989
8.

Huntington's disease: progress toward effective disease-modifying treatments and a cure.

Johnson CD, Davidson BL.

Hum Mol Genet. 2010 Apr 15;19(R1):R98-R102. doi: 10.1093/hmg/ddq148. Epub 2010 Apr 26. Review.

9.

Oligonucleotide-based strategies to combat polyglutamine diseases.

Fiszer A, Krzyzosiak WJ.

Nucleic Acids Res. 2014 Jun;42(11):6787-810. doi: 10.1093/nar/gku385. Epub 2014 May 21. Review.

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