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Items: 1 to 20 of 39

1.

Neonatal bone marrow transplantation of ADA-deficient SCID mice results in immunologic reconstitution despite low levels of engraftment and an absence of selective donor T lymphoid expansion.

Carbonaro DA, Jin X, Cotoi D, Mi T, Yu XJ, Skelton DC, Dorey F, Kellems RE, Blackburn MR, Kohn DB.

Blood. 2008 Jun 15;111(12):5745-54. doi: 10.1182/blood-2007-08-103663. Epub 2008 Mar 20.

2.

Update on gene therapy for adenosine deaminase-deficient severe combined immunodeficiency.

Ferrua F, Brigida I, Aiuti A.

Curr Opin Allergy Clin Immunol. 2010 Dec;10(6):551-6. doi: 10.1097/ACI.0b013e32833fea85. Review.

PMID:
20966749
3.

[Transplantation of genetically modified cells in the treatment of children with SCID: great hopes and recent disappointments].

Smogorzewska EM, Weinberg KI, Kohn DB.

Med Wieku Rozwoj. 2003 Jan-Mar;7(1):27-34. Review. Polish.

PMID:
13130167
4.

B-cell reconstitution for SCID: should a conditioning regimen be used in SCID treatment?

Haddad E, Leroy S, Buckley RH.

J Allergy Clin Immunol. 2013 Apr;131(4):994-1000. doi: 10.1016/j.jaci.2013.01.047. Epub 2013 Mar 5. Review.

5.

Relationship between patterns of engraftment in peripheral blood and immune reconstitution after allogeneic bone marrow transplantation for (severe) combined immunodeficiency.

van Leeuwen JE, van Tol MJ, Joosten AM, Schellekens PT, van den Bergh RL, Waaijer JL, Oudeman-Gruber NJ, van der Weijden-Ragas CP, Roos MT, Gerritsen EJ, et al.

Blood. 1994 Dec 1;84(11):3936-47. Review.

6.

Development of gene therapy for immunodeficiency: adenosine deaminase deficiency.

Blaese RM.

Pediatr Res. 1993 Jan;33(1 Suppl):S49-53; discussion S53-5. Review.

PMID:
8433875
7.

Bone marrow transplantation and alternatives for adenosine deaminase deficiency.

Gaspar HB.

Immunol Allergy Clin North Am. 2010 May;30(2):221-36. doi: 10.1016/j.iac.2010.01.002. Review.

PMID:
20493398
8.

Bone marrow gene therapy for adenosine deaminase deficiency.

Kaptein LC, Einerhand MP, Braakman E, Valerio D, van Beusechem VW.

Immunodeficiency. 1993;4(1-4):335-45. Review.

PMID:
7909479
9.

Gene therapy for severe combined immunodeficiencies.

Gaspar HB, Thrasher AJ.

Expert Opin Biol Ther. 2005 Sep;5(9):1175-82. Review.

PMID:
16120048
10.

Allogeneic bone marrow transplantation: relation between chimaerism and immunity.

Vossen J.

Verh K Acad Geneeskd Belg. 1998;60(2):111-43; discussion 143-5. Review.

PMID:
9703764
11.

New insights into the pathogenesis of adenosine deaminase-severe combined immunodeficiency and progress in gene therapy.

Sauer AV, Aiuti A.

Curr Opin Allergy Clin Immunol. 2009 Dec;9(6):496-502. doi: 10.1097/ACI.0b013e3283327da5. Review.

PMID:
19779332
12.

Adenosine Deaminase Deficiency.

Hershfield M.

In: Pagon RA, Adam MP, Ardinger HH, Wallace SE, Amemiya A, Bean LJH, Bird TD, Ledbetter N, Mefford HC, Smith RJH, Stephens K, editors. GeneReviews® [Internet]. Seattle (WA): University of Washington, Seattle; 1993-2017.
2006 Oct 3 [updated 2017 Mar 16].

13.

Gene therapy for adenosine deaminase deficiency.

Aiuti A, Ficara F, Cattaneo F, Bordignon C, Roncarolo MG.

Curr Opin Allergy Clin Immunol. 2003 Dec;3(6):461-6. Review.

PMID:
14612670
14.

Advances in gene therapy for ADA-deficient SCID.

Aiuti A.

Curr Opin Mol Ther. 2002 Oct;4(5):515-22. Review.

PMID:
12435054
15.

Management options for adenosine deaminase deficiency; proceedings of the EBMT satellite workshop (Hamburg, March 2006).

Booth C, Hershfield M, Notarangelo L, Buckley R, Hoenig M, Mahlaoui N, Cavazzana-Calvo M, Aiuti A, Gaspar HB.

Clin Immunol. 2007 May;123(2):139-47. Epub 2007 Feb 14. Review.

PMID:
17300989
17.

Gene therapy for adenosine deaminase deficiency.

Cappelli B, Aiuti A.

Immunol Allergy Clin North Am. 2010 May;30(2):249-60. doi: 10.1016/j.iac.2010.02.003. Review.

PMID:
20493400
18.

Adenosine deaminase: functional implications and different classes of inhibitors.

Cristalli G, Costanzi S, Lambertucci C, Lupidi G, Vittori S, Volpini R, Camaioni E.

Med Res Rev. 2001 Mar;21(2):105-28. Review.

PMID:
11223861
19.

How I treat ADA deficiency.

Gaspar HB, Aiuti A, Porta F, Candotti F, Hershfield MS, Notarangelo LD.

Blood. 2009 Oct 22;114(17):3524-32. doi: 10.1182/blood-2009-06-189209. Epub 2009 Jul 28. Review.

20.

Transplantation of hematopoietic stem cells in human severe combined immunodeficiency: longterm outcomes.

Buckley RH.

Immunol Res. 2011 Apr;49(1-3):25-43. doi: 10.1007/s12026-010-8191-9. Review.

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