Format
Sort by
Items per page

Send to

Choose Destination

Links from PubMed

Items: 15

1.

Globin lentiviral vector insertions can perturb the expression of endogenous genes in beta-thalassemic hematopoietic cells.

Hargrove PW, Kepes S, Hanawa H, Obenauer JC, Pei D, Cheng C, Gray JT, Neale G, Persons DA.

Mol Ther. 2008 Mar;16(3):525-33. doi: 10.1038/sj.mt.6300394. Epub 2008 Jan 15.

2.

Progress toward the genetic treatment of the beta-thalassemias.

Sadelain M, Lisowski L, Samakoglu S, Rivella S, May C, Riviere I.

Ann N Y Acad Sci. 2005;1054:78-91. Review.

PMID:
16339654
4.

Hematopoietic stem cell gene transfer for the treatment of hemoglobin disorders.

Persons DA.

Hematology Am Soc Hematol Educ Program. 2009:690-7. doi: 10.1182/asheducation-2009.1.690. Review.

PMID:
20008255
5.

Therapeutic globin gene delivery using lentiviral vectors.

Rivella S, Sadelain M.

Curr Opin Mol Ther. 2002 Oct;4(5):505-14. Review.

PMID:
12435053
6.
7.

Current status of globin gene therapy for the treatment of beta-thalassaemia.

Lisowski L, Sadelain M.

Br J Haematol. 2008 May;141(3):335-45. doi: 10.1111/j.1365-2141.2008.07098.x. Review.

PMID:
18410569
8.

The beta-globin locus control region versus gene therapy vectors: a struggle for expression.

Ellis J, Pannell D.

Clin Genet. 2001 Jan;59(1):17-24. Review.

PMID:
11168020
9.

Current advances in retroviral gene therapy.

Yi Y, Noh MJ, Lee KH.

Curr Gene Ther. 2011 Jun;11(3):218-28. Review.

10.

Globin gene transfer for treatment of the beta-thalassemias and sickle cell disease.

Sadelain M, Rivella S, Lisowski L, Samakoglu S, Rivière I.

Best Pract Res Clin Haematol. 2004 Sep;17(3):517-34. Review.

PMID:
15498721
11.

Gene therapy using retrovirus vectors: vector development and biosafety at clinical trials.

Doi K, Takeuchi Y.

Uirusu. 2015;65(1):27-36. doi: 10.2222/jsv.65.27. Review. Japanese.

13.

Development of gene therapy for thalassemia.

Nienhuis AW, Persons DA.

Cold Spring Harb Perspect Med. 2012 Nov 1;2(11). pii: a011833. doi: 10.1101/cshperspect.a011833. Review.

14.

Cell and Gene Therapy for the Beta-Thalassemias: Advances and Prospects.

Mansilla-Soto J, Riviere I, Boulad F, Sadelain M.

Hum Gene Ther. 2016 Apr;27(4):295-304. doi: 10.1089/hum.2016.037. Review.

15.

Analyzing the Genotoxicity of Retroviral Vectors in Hematopoietic Cell Gene Therapy.

Biasco L, Rothe M, Büning H, Schambach A.

Mol Ther Methods Clin Dev. 2017 Oct 5;8:21-30. doi: 10.1016/j.omtm.2017.10.002. eCollection 2018 Mar 16. Review.

Supplemental Content

Support Center