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Items: 1 to 20 of 110

1.

Update on treatment of lysosomal storage diseases.

Bruni S, Loschi L, Incerti C, Gabrielli O, Coppa GV.

Acta Myol. 2007 Jul;26(1):87-92. Review.

2.

[Treatment prospects of lysosomal storage disorders].

Reismann P, Tulassay Z.

Orv Hetil. 2008 Jun 22;149(25):1171-9. doi: 10.1556/OH.2008.28382. Review. Hungarian.

PMID:
18547894
3.
4.

Recent developments in therapeutic approaches for lysosomal storage diseases.

Urbanelli L, Magini A, Polchi A, Polidoro M, Emiliani C.

Recent Pat CNS Drug Discov. 2011 Jan;6(1):1-19. Review.

PMID:
21073432
5.

New strategies for the treatment of lysosomal storage diseases (review).

Parenti G, Pignata C, Vajro P, Salerno M.

Int J Mol Med. 2013 Jan;31(1):11-20. doi: 10.3892/ijmm.2012.1187. Epub 2012 Nov 19. Review.

PMID:
23165354
6.

[Lysosomes and lysosomal storage diseases].

Germain DP.

J Soc Biol. 2002;196(2):127-34. Review. French.

PMID:
12360741
7.

CNS-directed gene therapy for lysosomal storage diseases.

Sands MS, Haskins ME.

Acta Paediatr. 2008 Apr;97(457):22-7. doi: 10.1111/j.1651-2227.2008.00660.x. Review.

8.

Gene transfer strategies for correction of lysosomal storage disorders.

D'Azzo A.

Acta Haematol. 2003;110(2-3):71-85. Review.

PMID:
14583667
9.

Lysosomal storage diseases: mechanisms of enzyme replacement therapy.

Bou-Gharios G, Abraham D, Olsen I.

Histochem J. 1993 Sep;25(9):593-605. Review.

PMID:
8226100
10.

[Lysosomal storage diseases: functional classification and treatment principles].

Maire I.

Presse Med. 2007 Mar;36 Spec No 1:1S88-95. Review. French.

PMID:
17546775
11.

Current strategies in the management of lysosomal storage diseases.

Heese BA.

Semin Pediatr Neurol. 2008 Sep;15(3):119-26. doi: 10.1016/j.spen.2008.05.005. Review.

PMID:
18708002
12.

Combination Therapies for Lysosomal Storage Diseases: A Complex Answer to a Simple Problem.

Macauley SL.

Pediatr Endocrinol Rev. 2016 Jun;13 Suppl 1:639-48. Review.

13.

Therapeutic approaches for lysosomal storage diseases: a patent update.

Urbanelli L, Sagini K, Polidoro M, Brozzi A, Magini A, Emiliani C.

Recent Pat CNS Drug Discov. 2013 Aug;8(2):91-109. Review.

PMID:
23713988
14.

Gene therapy for lysosomal storage diseases: progress, challenges and future prospects.

Seregin SS, Amalfitano A.

Curr Pharm Des. 2011;17(24):2558-74. Review.

PMID:
21774776
15.

Lysosomal storage diseases: from pathophysiology to therapy.

Parenti G, Andria G, Ballabio A.

Annu Rev Med. 2015;66:471-86. doi: 10.1146/annurev-med-122313-085916. Review.

PMID:
25587658
16.
17.

Gene therapy for lysosomal storage disorders.

Ioannou YA, Enriquez A, Benjamin C.

Expert Opin Biol Ther. 2003 Aug;3(5):789-801. Review.

PMID:
12880379
18.

A review of gene therapy in canine and feline models of lysosomal storage disorders.

Bradbury AM, Gurda BL, Casal ML, Ponder KP, Vite CH, Haskins ME.

Hum Gene Ther Clin Dev. 2015 Mar;26(1):27-37. doi: 10.1089/humc.2015.002. Epub 2015 Feb 11. Review.

19.

[Therapy of lysosomal storage diseases: update and perspectives].

Lara-Aguilar RA, Juárez-Vázquez CI, Medina-Lozano C.

Rev Invest Clin. 2011 Nov-Dec;63(6):651-8. Review. Spanish.

PMID:
23650678
20.

Combination therapies for lysosomal storage disease: is the whole greater than the sum of its parts?

Hawkins-Salsbury JA, Reddy AS, Sands MS.

Hum Mol Genet. 2011 Apr 15;20(R1):R54-60. doi: 10.1093/hmg/ddr112. Epub 2011 Mar 19. Review.

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