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Items: 1 to 20 of 34

1.

Efficient hepatic delivery and expression from a recombinant adeno-associated virus 8 pseudotyped alpha1-antitrypsin vector.

Conlon TJ, Cossette T, Erger K, Choi YK, Clarke T, Scott-Jorgensen M, Song S, Campbell-Thompson M, Crawford J, Flotte TR.

Mol Ther. 2005 Nov;12(5):867-75. Epub 2005 Aug 8.

2.

Gene therapy progress and prospects: alpha-1 antitrypsin.

Stecenko AA, Brigham KL.

Gene Ther. 2003 Jan;10(2):95-9. Review.

PMID:
12571637
3.

Current status of gene therapy for α-1 antitrypsin deficiency.

Loring HS, Flotte TR.

Expert Opin Biol Ther. 2015 Mar;15(3):329-36. doi: 10.1517/14712598.2015.978854. Epub 2014 Nov 3. Review.

PMID:
25363251
4.

Clinical gene therapy using recombinant adeno-associated virus vectors.

Mueller C, Flotte TR.

Gene Ther. 2008 Jun;15(11):858-63. doi: 10.1038/gt.2008.68. Epub 2008 Apr 17. Review.

PMID:
18418415
5.

Intrapleural 'outside-in' gene therapy: therapeutics for organs of the chest via gene transfer to the pleura.

Heguy A, Crystal RG.

Curr Opin Mol Ther. 2005 Oct;7(5):440-53. Review.

PMID:
16248279
6.

Genetic control of human alpha-1-antitrypsin.

Sifers RN, Shen RF, Woo SL.

Mol Biol Med. 1989 Apr;6(2):127-35. Review.

PMID:
2693888
7.

Emphysema in alpha1-antitrypsin deficiency: does replacement therapy affect outcome?

Abboud RT, Ford GT, Chapman KR.

Treat Respir Med. 2005;4(1):1-8. Review.

PMID:
15725045
8.

The role of proteases, endoplasmic reticulum stress and SERPINA1 heterozygosity in lung disease and α-1 anti-trypsin deficiency.

Greene CM, Hassan T, Molloy K, McElvaney NG.

Expert Rev Respir Med. 2011 Jun;5(3):395-411. doi: 10.1586/ers.11.20. Review.

PMID:
21702661
9.

The discovery of α1-antitrypsin and its role in health and disease.

Janciauskiene SM, Bals R, Koczulla R, Vogelmeier C, Köhnlein T, Welte T.

Respir Med. 2011 Aug;105(8):1129-39. doi: 10.1016/j.rmed.2011.02.002. Epub 2011 Mar 1. Review.

10.

Liver disease in alpha-1 antitrypsin deficiency: current understanding and future therapy.

Teckman JH.

COPD. 2013 Mar;10 Suppl 1:35-43. doi: 10.3109/15412555.2013.765839. Review.

PMID:
23527737
11.
12.

Gene-based therapy for alpha-1 antitrypsin deficiency.

Mueller C, Flotte TR.

COPD. 2013 Mar;10 Suppl 1:44-9. doi: 10.3109/15412555.2013.764978. Review.

PMID:
23527792
13.

Challenges and Prospects for Alpha-1 Antitrypsin Deficiency Gene Therapy.

Wozniak J, Wandtke T, Kopinski P, Chorostowska-Wynimko J.

Hum Gene Ther. 2015 Nov;26(11):709-18. doi: 10.1089/hum.2015.044. Epub 2015 Sep 29. Review.

14.

Alpha-1 antitrypsin deficiency is not a rare disease but a disease that is rarely diagnosed.

de Serres FJ.

Environ Health Perspect. 2003 Dec;111(16):1851-4. Review.

15.

Gene Therapy for Alpha-1 Antitrypsin Deficiency Lung Disease.

Chiuchiolo MJ, Crystal RG.

Ann Am Thorac Soc. 2016 Aug;13 Suppl 4:S352-69. doi: 10.1513/AnnalsATS.201506-344KV. Review.

16.

Molecular biology and genetics of alpha 1-antitrypsin deficiency.

Sifers RN, Finegold MJ, Woo SL.

Semin Liver Dis. 1992 Aug;12(3):301-10. Review.

PMID:
1439881
17.

Gene therapy for alpha-1 antitrypsin deficiency.

Flotte TR, Mueller C.

Hum Mol Genet. 2011 Apr 15;20(R1):R87-92. doi: 10.1093/hmg/ddr156. Epub 2011 Apr 16. Review.

18.

Alpha1-antitrypsin deficiency. 1: epidemiology of alpha1-antitrypsin deficiency.

Luisetti M, Seersholm N.

Thorax. 2004 Feb;59(2):164-9. Review.

19.

The promise of gene therapy for the treatment of alpha-1 antitrypsin deficiency.

Cruz PE, Mueller C, Flotte TR.

Pharmacogenomics. 2007 Sep;8(9):1191-8. Review.

PMID:
17924834
20.

[Clinical consequences and diagnosis of congenital alpha 1-antitrypsin deficiency].

Lipska A, Wysocka J.

Przegl Lek. 1998;55(10):537-41. Review. Polish.

PMID:
10224869

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