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Items: 1 to 20 of 368

1.

Successful peripheral T-lymphocyte-directed gene transfer for a patient with severe combined immune deficiency caused by adenosine deaminase deficiency.

Onodera M, Ariga T, Kawamura N, Kobayashi I, Ohtsu M, Yamada M, Tame A, Furuta H, Okano M, Matsumoto S, Kotani H, McGarrity GJ, Blaese RM, Sakiyama Y.

Blood. 1998 Jan 1;91(1):30-6.

2.

[Study of T cell-directed gene transfer for a patient with ADA deficiency].

Sakiyama Y, Ariga T, Kawamura N.

Nihon Rinsho. 1998 Mar;56(3):696-700. Review. Japanese.

PMID:
9549359
3.

[Gene therapy for adenosine deaminase deficiency].

Sakiyama Y.

Hokkaido Igaku Zasshi. 1996 Jan;71(1):27-32. Review. Japanese.

PMID:
8727372
4.

[The gene therapy for a patient with ADA deficiency; report of the first gene therapy trial in Japan].

Ariga T, Kawamura N, Sakiyama Y.

Nihon Rinsho. 1997 Jun;55(6):1572-9. Review. Japanese.

PMID:
9200950
5.

Successful reconstitution of immunity in ADA-SCID by stem cell gene therapy following cessation of PEG-ADA and use of mild preconditioning.

Gaspar HB, Bjorkegren E, Parsley K, Gilmour KC, King D, Sinclair J, Zhang F, Giannakopoulos A, Adams S, Fairbanks LD, Gaspar J, Henderson L, Xu-Bayford JH, Davies EG, Veys PA, Kinnon C, Thrasher AJ.

Mol Ther. 2006 Oct;14(4):505-13. Epub 2006 Aug 14.

6.

Transfer of the ADA gene into human ADA-deficient T lymphocytes reconstitutes specific immune functions.

Ferrari G, Rossini S, Nobili N, Maggioni D, Garofalo A, Giavazzi R, Mavilio F, Bordignon C.

Blood. 1992 Sep 1;80(5):1120-4.

7.

Recombinant adeno-associated virus-mediated gene transfer for the potential therapy of adenosine deaminase-deficient severe combined immune deficiency.

Silver JN, Elder M, Conlon T, Cruz P, Wright AJ, Srivastava A, Flotte TR.

Hum Gene Ther. 2011 Aug;22(8):935-49. doi: 10.1089/hum.2010.121. Epub 2011 Mar 13.

PMID:
21142972
8.

Bone marrow gene therapy for adenosine deaminase deficiency.

Kaptein LC, Einerhand MP, Braakman E, Valerio D, van Beusechem VW.

Immunodeficiency. 1993;4(1-4):335-45. Review.

PMID:
7909479
9.

In vivo kinetics of transduced cells in peripheral T cell-directed gene therapy: role of CD8+ cells in improved immunological function in an adenosine deaminase (ADA)-SCID patient.

Kawamura N, Ariga T, Ohtsu M, Kobayashi I, Yamada M, Tame A, Furuta H, Okano M, Egashira M, Niikawa N, Kobayashi K, Sakiyama Y.

J Immunol. 1999 Aug 15;163(4):2256-61.

10.

Gene therapy for severe combined immunodeficiency caused by adenosine deaminase deficiency: improved retroviral vectors for clinical trials.

Onodera M, Nelson DM, Sakiyama Y, Candotti F, Blaese RM.

Acta Haematol. 1999;101(2):89-96. Review.

PMID:
10202239
11.

Adenosine deaminase deficiency as the first target disorder in gene therapy.

Onodera M, Sakiyama Y.

Expert Opin Investig Drugs. 2000 Mar;9(3):543-9. Review.

PMID:
11060694
12.

Bone marrow gene transfer in three patients with adenosine deaminase deficiency.

Hoogerbrugge PM, van Beusechem VW, Fischer A, Debree M, le Deist F, Perignon JL, Morgan G, Gaspar B, Fairbanks LD, Skeoch CH, Moseley A, Harvey M, Levinsky RJ, Valerio D.

Gene Ther. 1996 Feb;3(2):179-83.

PMID:
8867866
13.

Adenosine deaminase deficiency: clinical expression, molecular basis, and therapy.

Hershfield MS.

Semin Hematol. 1998 Oct;35(4):291-8. Review.

PMID:
9801258
14.

Gene therapy for severe combined immunodeficiencies.

Gaspar HB, Thrasher AJ.

Expert Opin Biol Ther. 2005 Sep;5(9):1175-82. Review.

PMID:
16120048
15.

Gene therapy for adenosine deaminase deficiency.

Aiuti A, Ficara F, Cattaneo F, Bordignon C, Roncarolo MG.

Curr Opin Allergy Clin Immunol. 2003 Dec;3(6):461-6. Review.

PMID:
14612670
17.

Retroviral-mediated gene transfer into mammalian cells.

Kohn DB, Kantoff PW, Eglitis MA, McLachlin JR, Moen RC, Karson E, Zwiebel JA, Nienhuis A, Karlsson S, O'Reilly R, et al.

Blood Cells. 1987;13(1-2):285-98. Review.

PMID:
3311223
18.

Correction of adenosine deaminase deficiency in cultured human T and B cells by retrovirus-mediated gene transfer.

Kantoff PW, Kohn DB, Mitsuya H, Armentano D, Sieberg M, Zwiebel JA, Eglitis MA, McLachlin JR, Wiginton DA, Hutton JJ, et al.

Proc Natl Acad Sci U S A. 1986 Sep;83(17):6563-7.

19.

Elevation of serum IgE level and peripheral eosinophil count during T lymphocyte-directed gene therapy for ADA deficiency: implication of Tc2-like cells after gene transduction procedure.

Kawamura N, Ariga T, Ohtsu M, Yamada M, Tame A, Furuta H, Kobayashi I, Okano M, Yanagihara Y, Sakiyama Y.

Immunol Lett. 1998 Nov;64(1):49-53.

PMID:
9865602
20.

[Gene therapy for adenosine deaminase deficiency].

Sakiyama Y, Ariga T, Ohtsu M.

Nihon Rinsho. 2005 Mar;63(3):448-52. Review. Japanese.

PMID:
15773344

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