Similar articles for PMID: 31971453

Year	Number of Results
1993	1
1995	1
1996	3
1998	2
2000	2
2001	2
2002	1
2003	1
2004	2
2005	2
2006	2
2007	1
2008	3
2009	5
2010	2
2011	6
2012	5
2013	7
2014	1
2015	5
2016	7
2017	14
2018	9
2019	10
2020	17
2021	23
2022	16
2023	7
2024	0

1

Assessing the potential cost-effectiveness of a gene therapy for the treatment of hemophilia A.

Cook K, Forbes SP, Adamski K, Ma JJ, Chawla A, Garrison LP Jr. Cook K, et al. J Med Econ. 2020 May;23(5):501-512. doi: 10.1080/13696998.2020.1721508. Epub 2020 Feb 13. J Med Econ. 2020. PMID: 31971453 Free article.

2

Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A.

Ozelo MC, Mahlangu J, Pasi KJ, Giermasz A, Leavitt AD, Laffan M, Symington E, Quon DV, Wang JD, Peerlinck K, Pipe SW, Madan B, Key NS, Pierce GF, O'Mahony B, Kaczmarek R, Henshaw J, Lawal A, Jayaram K, Huang M, Yang X, Wong WY, Kim B; GENEr8-1 Trial Group. Ozelo MC, et al. N Engl J Med. 2022 Mar 17;386(11):1013-1025. doi: 10.1056/NEJMoa2113708. N Engl J Med. 2022. PMID: 35294811 Clinical Trial.

3

Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A.

Mahlangu J, Kaczmarek R, von Drygalski A, Shapiro S, Chou SC, Ozelo MC, Kenet G, Peyvandi F, Wang M, Madan B, Key NS, Laffan M, Dunn AL, Mason J, Quon DV, Symington E, Leavitt AD, Oldenburg J, Chambost H, Reding MT, Jayaram K, Yu H, Mahajan R, Chavele KM, Reddy DB, Henshaw J, Robinson TM, Wong WY, Pipe SW; GENEr8-1 Trial Group. Mahlangu J, et al. N Engl J Med. 2023 Feb 23;388(8):694-705. doi: 10.1056/NEJMoa2211075. N Engl J Med. 2023. PMID: 36812433 Clinical Trial.

4

Hemophilia Gene Therapy Value Assessment: Methodological Challenges and Recommendations.

Garrison LP, Pezalla E, Towse A, Yang H, Faust E, Wu EQ, Li N, Sawyer EK, Recht M. Garrison LP, et al. Value Health. 2021 Nov;24(11):1628-1633. doi: 10.1016/j.jval.2021.05.008. Epub 2021 Oct 3. Value Health. 2021. PMID: 34711363 Free article.

5

Economic evaluation of major knee surgery with recombinant activated factor VII in hemophilia patients with high titer inhibitors and advanced knee arthropathy: exploratory results via literature-based modeling.

Ballal RD, Botteman MF, Foley I, Stephens JM, Wilke CT, Joshi AV. Ballal RD, et al. Curr Med Res Opin. 2008 Mar;24(3):753-68. doi: 10.1185/030079908X273048. Epub 2008 Jan 29. Curr Med Res Opin. 2008. PMID: 18234151

6

Persistence of haemostatic response following gene therapy with valoctocogene roxaparvovec in severe haemophilia A.

Pasi KJ, Laffan M, Rangarajan S, Robinson TM, Mitchell N, Lester W, Symington E, Madan B, Yang X, Kim B, Pierce GF, Wong WY. Pasi KJ, et al. Haemophilia. 2021 Nov;27(6):947-956. doi: 10.1111/hae.14391. Epub 2021 Aug 11. Haemophilia. 2021. PMID: 34378280 Free PMC article.

7

Valoctocogene Roxaparvovec: First Approval.

Blair HA. Blair HA. Drugs. 2022 Sep;82(14):1505-1510. doi: 10.1007/s40265-022-01788-y. Drugs. 2022. PMID: 36214970 Review.

8

Cost-utility analysis of life-long prophylaxis with recombinant factor VIIIFc vs recombinant factor VIII for the management of severe hemophilia A in Sweden.

Henry N, Jovanović J, Schlueter M, Kritikou P, Wilson K, Myrén KJ. Henry N, et al. J Med Econ. 2018 Apr;21(4):318-325. doi: 10.1080/13696998.2017.1405816. Epub 2017 Dec 4. J Med Econ. 2018. PMID: 29139314 Free article. Clinical Trial.

9

A Budget Impact Model of Hemophilia Bypassing Agent Prophylaxis Relative to Recombinant Factor VIIa On-Demand.

Mehta DA, Oladapo AO, Epstein JD, Novack AR, Neufeld EJ, Hay JW. Mehta DA, et al. J Manag Care Spec Pharm. 2016 Feb;22(2):149-57. doi: 10.18553/jmcp.2016.22.2.149. J Manag Care Spec Pharm. 2016. PMID: 27015254 Free PMC article.

10

Gene therapy in hemophilia A: a cost-effectiveness analysis.

Machin N, Ragni MV, Smith KJ. Machin N, et al. Blood Adv. 2018 Jul 24;2(14):1792-1798. doi: 10.1182/bloodadvances.2018021345. Blood Adv. 2018. PMID: 30042145 Free PMC article.

Save citations to file

Email citations

Send citations to clipboard

Add to Collections

Add to My Bibliography

Create a file for external citation management software

Your saved search

Your RSS Feed

My NCBI Filters

Results by year

Text availability

Article attribute

Article type

Publication date

139 results

Results by year