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Items: 1 to 20 of 98

1.

Hyperactive Factor IX Padua: A Game-Changer for Hemophilia Gene Therapy.

VandenDriessche T, Chuah MK.

Mol Ther. 2018 Jan 3;26(1):14-16. doi: 10.1016/j.ymthe.2017.12.007. Epub 2017 Dec 21. No abstract available.

2.

Gene therapy. Factor IX Padua: them that have, give.

Lozier JN.

Blood. 2012 Nov 29;120(23):4452-3. doi: 10.1182/blood-2012-09-452821.

3.

Hemophilia Gene Therapy: Ready for Prime Time?

VandenDriessche T, Chuah MK.

Hum Gene Ther. 2017 Nov;28(11):1013-1023. doi: 10.1089/hum.2017.116. Epub 2017 Aug 3. Review.

PMID:
28793786
4.

Hemophilia gene therapy is effective and safe.

Makris M.

Blood. 2018 Mar 1;131(9):952-953. doi: 10.1182/blood-2018-01-824144. No abstract available.

5.

Gene therapy for hemophilia: the clot thickens.

High KA.

Hum Gene Ther. 2014 Nov;25(11):915-22. doi: 10.1089/hum.2014.2541. No abstract available.

6.

The molecular genetics of hemophilia A and B in man. Factor VIII and factor IX deficiency.

Antonarakis SE.

Adv Hum Genet. 1988;17:27-59. Review. No abstract available.

PMID:
3142226
7.

Gene therapy: Genie in a vector.

Gould J.

Nature. 2014 Nov 27;515(7528):S160-1. doi: 10.1038/515S160a. No abstract available.

PMID:
25427205
8.

Genie in a vector.

Gould J.

Sci Am. 2015 Jan;312(1):S6-7. No abstract available.

PMID:
25597116
9.

Gene Therapy for Hemophilia.

Nienhuis AW, Nathwani AC, Davidoff AM.

Mol Ther. 2017 May 3;25(5):1163-1167. doi: 10.1016/j.ymthe.2017.03.033. Epub 2017 Apr 11. Review.

10.

The fix is in.

Pemberton S.

Sci Am. 2015 Jan;312(1):S11. No abstract available.

PMID:
25597118
11.

A golden age for Haemophilia treatment?

Makris M, Hermans C.

Haemophilia. 2018 Mar;24(2):175-176. doi: 10.1111/hae.13411. No abstract available.

PMID:
29601683
12.

Gene Therapy for Hemophilia.

Nathwani AC, Davidoff AM, Tuddenham EGD.

Hematol Oncol Clin North Am. 2017 Oct;31(5):853-868. doi: 10.1016/j.hoc.2017.06.011. Review.

PMID:
28895852
13.

[Structure and function of factor VIII and factor IX gene and molecular DNA diagnosis in hemophilia A and B].

Herrmann FH, Wehnert M, Wulff K.

Z Arztl Fortbild (Jena). 1988;82(22):1116-22. Review. German. No abstract available.

PMID:
2907834
14.

Advances in Gene Therapy for Hemophilia.

Nathwani AC, Davidoff AM, Tuddenham EGD.

Hum Gene Ther. 2017 Nov;28(11):1004-1012. doi: 10.1089/hum.2017.167. Review.

PMID:
28835123
15.

Gene therapy for haemophilia.

Pasi KJ.

Baillieres Clin Haematol. 1996 Jun;9(2):305-17. Review. No abstract available.

PMID:
8800507
16.

Our journey to successful gene therapy for hemophilia B.

Nathwani AC, Nienhuis AW, Davidoff AM.

Hum Gene Ther. 2014 Nov;25(11):923-6. doi: 10.1089/hum.2014.2540. No abstract available.

17.

Gene therapy in an era of emerging treatment options for hemophilia B.

Monahan PE.

J Thromb Haemost. 2015 Jun;13 Suppl 1:S151-60. doi: 10.1111/jth.12957. Review.

18.

A David promoter with Goliath strength.

Markusic DM, Herzog RW.

Blood. 2014 May 15;123(20):3068-9. doi: 10.1182/blood-2014-04-565507.

19.

Merry christmas for patients with hemophilia B.

Ponder KP.

N Engl J Med. 2011 Dec 22;365(25):2424-5. doi: 10.1056/NEJMe1111138. Epub 2011 Dec 10. No abstract available.

PMID:
22149960
20.

Status of gene transfer for hemophilia A and B.

Thompson AR.

Thromb Haemost. 1991 Jul 12;66(1):119-22. Review. No abstract available.

PMID:
1926041

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