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Items: 1 to 20 of 98

1.
2.

Enzyme replacement in the CSF to treat metachromatic leukodystrophy in mouse model using single intracerebroventricular injection of self-complementary AAV1 vector.

Hironaka K, Yamazaki Y, Hirai Y, Yamamoto M, Miyake N, Miyake K, Okada T, Morita A, Shimada T.

Sci Rep. 2015 Aug 18;5:13104. doi: 10.1038/srep13104.

5.

The ependymal route for insulin-like growth factor-1 gene therapy in the brain.

Hereñú CB, Sonntag WE, Morel GR, Portiansky EL, Goya RG.

Neuroscience. 2009 Sep 29;163(1):442-7. doi: 10.1016/j.neuroscience.2009.06.024. Epub 2009 Jun 13.

6.

Comparative efficacy and safety of multiple routes of direct CNS administration of adeno-associated virus gene transfer vector serotype rh.10 expressing the human arylsulfatase A cDNA to nonhuman primates.

Rosenberg JB, Sondhi D, Rubin DG, Monette S, Chen A, Cram S, De BP, Kaminsky SM, Sevin C, Aubourg P, Crystal RG.

Hum Gene Ther Clin Dev. 2014 Sep;25(3):164-77. doi: 10.1089/humc.2013.239. Epub 2014 Aug 21.

7.

Systemic hyperosmolality improves beta-glucuronidase distribution and pathology in murine MPS VII brain following intraventricular gene transfer.

Ghodsi A, Stein C, Derksen T, Martins I, Anderson RD, Davidson BL.

Exp Neurol. 1999 Nov;160(1):109-16.

PMID:
10630195
8.

Induction of tolerance to human arylsulfatase A in a mouse model of metachromatic leukodystrophy.

Matzner U, Matthes F, Herbst E, Lüllmann-Rauch R, Callaerts-Vegh Z, D'Hooge R, Weigelt C, Eistrup C, Fogh J, Gieselmann V.

Mol Med. 2007 Sep-Oct;13(9-10):471-9.

9.

Global diffuse distribution in the brain and efficient gene delivery to the dorsal root ganglia by intrathecal injection of adeno-associated viral vector serotype 1.

Iwamoto N, Watanabe A, Yamamoto M, Miyake N, Kurai T, Teramoto A, Shimada T.

J Gene Med. 2009 Jun;11(6):498-505. doi: 10.1002/jgm.1325.

PMID:
19338016
10.

Brain ischemia augments exo-focal transgene expression of adenovirus-mediated gene transfer to ependyma in hypertensive rats.

Kumai Y, Ooboshi H, Kitazono T, Takada J, Ibayashi S, Fujishima M, Iida M.

Exp Neurol. 2003 Dec;184(2):904-11.

PMID:
14769382
11.

A TAT-modified fusion protein efficiently penetrates mouse hypoglossal nuclei from transduced ependyma.

Alisky JM, Xia H, Davidson BL.

Neurosci Lett. 2006 Jun 19;401(1-2):40-3. Epub 2006 May 2.

PMID:
16650576
13.

Gene targeting in vivo by adeno-associated virus vectors.

Miller DG, Wang PR, Petek LM, Hirata RK, Sands MS, Russell DW.

Nat Biotechnol. 2006 Aug;24(8):1022-6. Epub 2006 Jul 30.

PMID:
16878127
15.
16.

Lentiviral vectors mediate efficient and stable gene transfer in adult neural stem cells in vivo.

Geraerts M, Eggermont K, Hernandez-Acosta P, Garcia-Verdugo JM, Baekelandt V, Debyser Z.

Hum Gene Ther. 2006 Jun;17(6):635-50.

PMID:
16776572
17.

Bone marrow stem cell gene therapy of arylsulfatase A-deficient mice, using an arylsulfatase A mutant that is hypersecreted from retrovirally transduced donor-type cells.

Matzner U, Schestag F, Hartmann D, Lüllmann-Rauch R, D'Hooge R, De Deyn PP, Gieselmann V.

Hum Gene Ther. 2001 Jun 10;12(9):1021-33.

PMID:
11399225
18.

Comparison of five peptide vectors for improved brain delivery of the lysosomal enzyme arylsulfatase A.

Böckenhoff A, Cramer S, Wölte P, Knieling S, Wohlenberg C, Gieselmann V, Galla HJ, Matzner U.

J Neurosci. 2014 Feb 26;34(9):3122-9. doi: 10.1523/JNEUROSCI.4785-13.2014.

19.

Transduction of the central nervous system after intracerebroventricular injection of adeno-associated viral vectors in neonatal and juvenile mice.

Gholizadeh S, Tharmalingam S, Macaldaz ME, Hampson DR.

Hum Gene Ther Methods. 2013 Aug;24(4):205-13. doi: 10.1089/hgtb.2013.076. Epub 2013 Aug 3.

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