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Items: 1 to 20 of 101

1.

Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: advances in biology and future directions for treatment.

Pai SY, Notarangelo LD.

Immunol Allergy Clin North Am. 2010 May;30(2):179-94. doi: 10.1016/j.iac.2010.02.001. Review.

2.

Current and emerging treatment options for Wiskott-Aldrich syndrome.

Worth AJ, Thrasher AJ.

Expert Rev Clin Immunol. 2015;11(9):1015-32. doi: 10.1586/1744666X.2015.1062366. Epub 2015 Jul 9. Review.

PMID:
26159751
3.

[Wiskott-Aldrich syndrome].

Gulácsy V, Maródi L.

Orv Hetil. 2008 Jul 20;149(29):1367-71. doi: 10.1556/OH.2008.28377. Review. Hungarian.

PMID:
18617469
4.

Stable mixed chimerism after hematopoietic stem cell transplantation in Wiskott-Aldrich syndrome.

Doğu F, Kurtuluş-Ulküer M, Bilge Y, Bozdoğan G, Ulküer U, Malhatun E, Ikincioğullari A, Babacan E.

Pediatr Transplant. 2006 May;10(3):395-9.

PMID:
16677369
5.

Wiskott-Aldrich syndrome; an x-linked primary immunodeficiency disease with unique and characteristic features.

Ariga T.

Allergol Int. 2012 Jun;61(2):183-9. doi: 10.2332/allergolint.11-RAI-0412. Epub 2012 Feb 25. Review.

6.

Wiskott-Aldrich syndrome.

Notarangelo LD, Miao CH, Ochs HD.

Curr Opin Hematol. 2008 Jan;15(1):30-6. Review.

PMID:
18043243
7.

Stem-cell gene therapy for the Wiskott-Aldrich syndrome.

Boztug K, Schmidt M, Schwarzer A, Banerjee PP, Díez IA, Dewey RA, Böhm M, Nowrouzi A, Ball CR, Glimm H, Naundorf S, Kühlcke K, Blasczyk R, Kondratenko I, Maródi L, Orange JS, von Kalle C, Klein C.

N Engl J Med. 2010 Nov 11;363(20):1918-27. doi: 10.1056/NEJMoa1003548.

8.

Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome.

Hacein-Bey Abina S, Gaspar HB, Blondeau J, Caccavelli L, Charrier S, Buckland K, Picard C, Six E, Himoudi N, Gilmour K, McNicol AM, Hara H, Xu-Bayford J, Rivat C, Touzot F, Mavilio F, Lim A, Treluyer JM, Héritier S, Lefrère F, Magalon J, Pengue-Koyi I, Honnet G, Blanche S, Sherman EA, Male F, Berry C, Malani N, Bushman FD, Fischer A, Thrasher AJ, Galy A, Cavazzana M.

JAMA. 2015 Apr 21;313(15):1550-63. doi: 10.1001/jama.2015.3253.

9.

The genotype of the original Wiskott phenotype.

Binder V, Albert MH, Kabus M, Bertone M, Meindl A, Belohradsky BH.

N Engl J Med. 2006 Oct 26;355(17):1790-3.

10.

Recent advances in understanding the pathophysiology of Wiskott-Aldrich syndrome.

Bosticardo M, Marangoni F, Aiuti A, Villa A, Grazia Roncarolo M.

Blood. 2009 Jun 18;113(25):6288-95. doi: 10.1182/blood-2008-12-115253. Epub 2009 Apr 7. Review.

11.

Wiskott-Aldrich syndrome: diagnosis, clinical and laboratory manifestations, and treatment.

Ochs HD, Filipovich AH, Veys P, Cowan MJ, Kapoor N.

Biol Blood Marrow Transplant. 2009 Jan;15(1 Suppl):84-90. doi: 10.1016/j.bbmt.2008.10.007. Review.

12.

Development of hematopoietic stem cell gene therapy for Wiskott-Aldrich syndrome.

Boztug K, Dewey RA, Klein C.

Curr Opin Mol Ther. 2006 Oct;8(5):390-5. Review.

PMID:
17078381
13.

New insights into the biology of Wiskott-Aldrich syndrome (WAS).

Thrasher AJ.

Hematology Am Soc Hematol Educ Program. 2009:132-8. doi: 10.1182/asheducation-2009.1.132. Review.

PMID:
20008191
14.

Successful allogeneic peripheral blood stem cell transplantation in Wiskott-Aldrich Syndrome Patients: first report in Thailand.

Hongeng S, Benjaponpitak S, Tardtong P, Varavithya W, Chuansumrit A, Chunharas A, Chaisiripoomkere W, Hathira P.

Asian Pac J Allergy Immunol. 2001 Sep;19(3):191-5.

15.

Cutaneous manifestations in patients with Wiskott-Aldrich syndrome submitted to haematopoietic stem cell transplantation.

Loyola Presa JG, de Carvalho VO, Morrisey LR, Bonfim CM, Abagge KT, Vasselai A, Marinoni LP.

Arch Dis Child. 2013 Apr;98(4):304-7. doi: 10.1136/archdischild-2011-300812. Epub 2013 Jan 23.

PMID:
23343520
16.

Gene therapy for the Wiskott-Aldrich syndrome.

Galy A, Thrasher AJ.

Curr Opin Allergy Clin Immunol. 2011 Dec;11(6):545-50. doi: 10.1097/ACI.0b013e32834c230c. Review.

PMID:
21971332
17.

Linking cellular activation to cytoskeletal reorganization: Wiskott-Aldrich syndrome as a model.

Stewart DM, Tian L, Nelson DL.

Curr Opin Allergy Clin Immunol. 2001 Dec;1(6):525-33. Review.

PMID:
11964736
18.
19.

A multiinstitutional survey of the Wiskott-Aldrich syndrome.

Sullivan KE, Mullen CA, Blaese RM, Winkelstein JA.

J Pediatr. 1994 Dec;125(6 Pt 1):876-85.

PMID:
7996359
20.

Unrelated partially matched peripheral blood stem cell transplantation with highly purified CD34+ cells in a child with Wiskott-Aldrich syndrome.

Schwinger W, Urban C, Lackner H, Kerbl R, Benesch M, Dornbusch HJ, Sovinz P, Schumm M, Handgretinger R.

Bone Marrow Transplant. 2000 Jul;26(2):235-7.

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