Format
Sort by

Send to

Choose Destination

Links from PubMed

Items: 1 to 20 of 113

1.

In vivo correction of ZAP-70 immunodeficiency by intrathymic gene transfer.

Adjali O, Marodon G, Steinberg M, Mongellaz C, Thomas-Vaslin V, Jacquet C, Taylor N, Klatzmann D.

J Clin Invest. 2005 Aug;115(8):2287-95.

2.
3.

Reconstitution of lymphoid development and function in ZAP-70-deficient mice following gene transfer into bone marrow cells.

Otsu M, Steinberg M, Ferrand C, Merida P, Rebouissou C, Tiberghien P, Taylor N, Candotti F, Noraz N.

Blood. 2002 Aug 15;100(4):1248-56.

4.

Intrathymic administration of hematopoietic progenitor cells enhances T cell reconstitution in ZAP-70 severe combined immunodeficiency.

Adjali O, Vicente RR, Ferrand C, Jacquet C, Mongellaz C, Tiberghien P, Chebli K, Zimmermann VS, Taylor N.

Proc Natl Acad Sci U S A. 2005 Sep 20;102(38):13586-91. Epub 2005 Sep 7.

5.

Stable and functional lymphoid reconstitution in artemis-deficient mice following lentiviral artemis gene transfer into hematopoietic stem cells.

Benjelloun F, Garrigue A, Demerens-de Chappedelaine C, Soulas-Sprauel P, Malassis-Séris M, Stockholm D, Hauer J, Blondeau J, Rivière J, Lim A, Le Lorc'h M, Romana S, Brousse N, Pâques F, Galy A, Charneau P, Fischer A, de Villartay JP, Cavazzana-Calvo M.

Mol Ther. 2008 Aug;16(8):1490-9. doi: 10.1038/mt.2008.118. Epub 2008 Jun 17.

PMID:
18560421
6.

Recombination-activating gene 1 (Rag1)-deficient mice with severe combined immunodeficiency treated with lentiviral gene therapy demonstrate autoimmune Omenn-like syndrome.

van Til NP, Sarwari R, Visser TP, Hauer J, Lagresle-Peyrou C, van der Velden G, Malshetty V, Cortes P, Jollet A, Danos O, Cassani B, Zhang F, Thrasher AJ, Fontana E, Poliani PL, Cavazzana M, Verstegen MM, Villa A, Wagemaker G.

J Allergy Clin Immunol. 2014 Apr;133(4):1116-23. doi: 10.1016/j.jaci.2013.10.009. Epub 2013 Dec 9.

PMID:
24332219
7.

Reconstitution of T cell receptor signaling in ZAP-70-deficient cells by retroviral transduction of the ZAP-70 gene.

Taylor N, Bacon KB, Smith S, Jahn T, Kadlecek TA, Uribe L, Kohn DB, Gelfand EW, Weiss A, Weinberg K.

J Exp Med. 1996 Nov 1;184(5):2031-6.

8.

Intrathymic progenitor cell transplantation across histocompatibility barriers results in the persistence of early thymic progenitors and T-cell differentiation.

de Barros SC, Vicente R, Chebli K, Jacquet C, Zimmermann VS, Taylor N.

Blood. 2013 Mar 14;121(11):2144-53. doi: 10.1182/blood-2012-08-447417. Epub 2013 Jan 10.

9.

Development of an enhanced B-specific lentiviral vector expressing BTK: a tool for gene therapy of XLA.

Moreau T, Barlogis V, Bardin F, Nunes JA, Calmels B, Chabannon C, Tonnelle C.

Gene Ther. 2008 Jun;15(12):942-52. doi: 10.1038/gt.2008.17. Epub 2008 Mar 6.

PMID:
18323795
10.

Retrovirus-mediated transduction of primary ZAP-70-deficient human T cells results in the selective growth advantage of gene-corrected cells: implications for gene therapy.

Steinberg M, Swainson L, Schwarz K, Boyer M, Friedrich W, Yssel H, Taylor N, Noraz N.

Gene Ther. 2000 Aug;7(16):1392-400.

11.

Absence of ZAP-70 prevents signaling through the antigen receptor on peripheral blood T cells but not on thymocytes.

Gelfand EW, Weinberg K, Mazer BD, Kadlecek TA, Weiss A.

J Exp Med. 1995 Oct 1;182(4):1057-65.

12.

ZAP-70 restoration in mice by in vivo thymic electroporation.

Irla M, Saade M, Kissenpfennig A, Poulin LF, Leserman L, Marche PN, Jouvin-Marche E, Berger F, Nguyen C.

PLoS One. 2008 Apr 30;3(4):e2059. doi: 10.1371/journal.pone.0002059.

13.

Clonal evidence for the transduction of CD34+ cells with lymphomyeloid differentiation potential and self-renewal capacity in the SCID-X1 gene therapy trial.

Schmidt M, Hacein-Bey-Abina S, Wissler M, Carlier F, Lim A, Prinz C, Glimm H, Andre-Schmutz I, Hue C, Garrigue A, Le Deist F, Lagresle C, Fischer A, Cavazzana-Calvo M, von Kalle C.

Blood. 2005 Apr 1;105(7):2699-706. Epub 2004 Dec 7.

14.

Intrathymic transplantation of bone marrow-derived progenitors provides long-term thymopoiesis.

Vicente R, Adjali O, Jacquet C, Zimmermann VS, Taylor N.

Blood. 2010 Mar 11;115(10):1913-20. doi: 10.1182/blood-2009-06-229724. Epub 2009 Dec 29.

15.

A new chance for SCID gene therapy.

Bordignon C.

Nat Med. 1998 Jan;4(1):19-20. No abstract available.

PMID:
9427599
16.

Gene therapy of RAG-2-/- mice: sustained correction of the immunodeficiency.

Yates F, Malassis-Séris M, Stockholm D, Bouneaud C, Larousserie F, Noguiez-Hellin P, Danos O, Kohn DB, Fischer A, de Villartay JP, Cavazzana-Calvo M.

Blood. 2002 Dec 1;100(12):3942-9. Epub 2002 Aug 22.

17.

Restoration of lymphocyte function in Janus kinase 3-deficient mice by retroviral-mediated gene transfer.

Bunting KD, Sangster MY, Ihle JN, Sorrentino BP.

Nat Med. 1998 Jan;4(1):58-64.

PMID:
9427607
18.

Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy.

Hacein-Bey-Abina S, Le Deist F, Carlier F, Bouneaud C, Hue C, De Villartay JP, Thrasher AJ, Wulffraat N, Sorensen R, Dupuis-Girod S, Fischer A, Davies EG, Kuis W, Leiva L, Cavazzana-Calvo M.

N Engl J Med. 2002 Apr 18;346(16):1185-93.

19.

Retroviral transduction of IL2RG into CD34(+) cells from X-linked severe combined immunodeficiency patients permits human T- and B-cell development in sheep chimeras.

Tsai EJ, Malech HL, Kirby MR, Hsu AP, Seidel NE, Porada CD, Zanjani ED, Bodine DM, Puck JM.

Blood. 2002 Jul 1;100(1):72-9.

20.

Update on gene therapy for adenosine deaminase-deficient severe combined immunodeficiency.

Ferrua F, Brigida I, Aiuti A.

Curr Opin Allergy Clin Immunol. 2010 Dec;10(6):551-6. doi: 10.1097/ACI.0b013e32833fea85. Review.

PMID:
20966749
Items per page

Supplemental Content

Write to the Help Desk