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Items: 1 to 20 of 406

1.

Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse.

Lu QL, Mann CJ, Lou F, Bou-Gharios G, Morris GE, Xue SA, Fletcher S, Partridge TA, Wilton SD.

Nat Med. 2003 Aug;9(8):1009-14. Epub 2003 Jul 6.

PMID:
12847521
2.

Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping.

Goyenvalle A, Vulin A, Fougerousse F, Leturcq F, Kaplan JC, Garcia L, Danos O.

Science. 2004 Dec 3;306(5702):1796-9. Epub 2004 Nov 4.

4.

Screening for antisense modulation of dystrophin pre-mRNA splicing.

Dickson G, Hill V, Graham IR.

Neuromuscul Disord. 2002 Oct;12 Suppl 1:S67-70. Review.

PMID:
12206799
5.
6.

Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles.

Lu QL, Rabinowitz A, Chen YC, Yokota T, Yin H, Alter J, Jadoon A, Bou-Gharios G, Partridge T.

Proc Natl Acad Sci U S A. 2005 Jan 4;102(1):198-203. Epub 2004 Dec 17.

8.

Specific removal of the nonsense mutation from the mdx dystrophin mRNA using antisense oligonucleotides.

Wilton SD, Lloyd F, Carville K, Fletcher S, Honeyman K, Agrawal S, Kole R.

Neuromuscul Disord. 1999 Jul;9(5):330-8.

PMID:
10407856
9.

Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology.

Alter J, Lou F, Rabinowitz A, Yin H, Rosenfeld J, Wilton SD, Partridge TA, Lu QL.

Nat Med. 2006 Feb;12(2):175-7. Epub 2006 Jan 29.

PMID:
16444267
10.

Enhanced in vivo delivery of antisense oligonucleotides to restore dystrophin expression in adult mdx mouse muscle.

Wells KE, Fletcher S, Mann CJ, Wilton SD, Wells DJ.

FEBS Lett. 2003 Sep 25;552(2-3):145-9.

11.

Induced dystrophin exon skipping in human muscle explants.

McClorey G, Fall AM, Moulton HM, Iversen PL, Rasko JE, Ryan M, Fletcher S, Wilton SD.

Neuromuscul Disord. 2006 Oct;16(9-10):583-90. Epub 2006 Aug 21.

PMID:
16919955
12.

Antisense oligonucleotide-induced exon skipping restores dystrophin expression in vitro in a canine model of DMD.

McClorey G, Moulton HM, Iversen PL, Fletcher S, Wilton SD.

Gene Ther. 2006 Oct;13(19):1373-81. Epub 2006 May 25.

PMID:
16724091
13.

Modification of splicing in the dystrophin gene in cultured Mdx muscle cells by antisense oligoribonucleotides.

Dunckley MG, Manoharan M, Villiet P, Eperon IC, Dickson G.

Hum Mol Genet. 1998 Jul;7(7):1083-90.

PMID:
9618164
14.

Mdx mice inducibly expressing dystrophin provide insights into the potential of gene therapy for duchenne muscular dystrophy.

Ahmad A, Brinson M, Hodges BL, Chamberlain JS, Amalfitano A.

Hum Mol Genet. 2000 Oct 12;9(17):2507-15.

PMID:
11030755
15.

Restoration of dystrophin expression in mdx muscle cells by chimeraplast-mediated exon skipping.

Bertoni C, Lau C, Rando TA.

Hum Mol Genet. 2003 May 15;12(10):1087-99.

PMID:
12719373
16.

Potential of oligonucleotide-mediated exon-skipping therapy for Duchenne muscular dystrophy.

Yokota T, Pistilli E, Duddy W, Nagaraju K.

Expert Opin Biol Ther. 2007 Jun;7(6):831-42. Review.

PMID:
17555369
17.

Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy.

Aartsma-Rus A, Janson AA, van Ommen GJ, van Deutekom JC.

BMC Med Genet. 2007 Jul 5;8:43.

18.

In vivo comparison of 2'-O-methyl phosphorothioate and morpholino antisense oligonucleotides for Duchenne muscular dystrophy exon skipping.

Heemskerk HA, de Winter CL, de Kimpe SJ, van Kuik-Romeijn P, Heuvelmans N, Platenburg GJ, van Ommen GJ, van Deutekom JC, Aartsma-Rus A.

J Gene Med. 2009 Mar;11(3):257-66. doi: 10.1002/jgm.1288.

PMID:
19140108
19.

Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy.

Aartsma-Rus A, Bremmer-Bout M, Janson AA, den Dunnen JT, van Ommen GJ, van Deutekom JC.

Neuromuscul Disord. 2002 Oct;12 Suppl 1:S71-7.

PMID:
12206800
20.

U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping.

Brun C, Suter D, Pauli C, Dunant P, Lochm├╝ller H, Burgunder JM, Sch├╝mperli D, Weis J.

Cell Mol Life Sci. 2003 Mar;60(3):557-66.

PMID:
12737315

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