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Items: 1 to 20 of 229

1.

Therapeutic levels of human factor VIII in mice implanted with encapsulated cells: potential for gene therapy of haemophilia A.

García-Martín C, Chuah MK, Van Damme A, Robinson KE, Vanzieleghem B, Saint-Remy JM, Gallardo D, Ofosu FA, Vandendriessche T, Hortelano G.

J Gene Med. 2002 Mar-Apr;4(2):215-23.

PMID:
11933222
2.
3.

Bone marrow mesenchymal cells for haemophilia A gene therapy using retroviral vectors with modified long-terminal repeats.

Van Damme A, Chuah MK, Dell'accio F, De Bari C, Luyten F, Collen D, VandenDriessche T.

Haemophilia. 2003 Jan;9(1):94-103. Erratum in: Haemophilia. 2003 May;9(3):345.

PMID:
12558785
4.

Ex vivo gene therapy for hemophilia A that enhances safe delivery and sustained in vivo factor VIII expression from lentivirally engineered endothelial progenitors.

Matsui H, Shibata M, Brown B, Labelle A, Hegadorn C, Andrews C, Hebbel RP, Galipeau J, Hough C, Lillicrap D.

Stem Cells. 2007 Oct;25(10):2660-9. Epub 2007 Jul 5.

5.

Encapsulated human primary myoblasts deliver functional hFIX in hemophilic mice.

Wen J, Xu N, Li A, Bourgeois J, Ofosu FA, Hortelano G.

J Gene Med. 2007 Nov;9(11):1002-10.

PMID:
17868187
6.

Recombinant factor VIII expression in hematopoietic cells following lentiviral transduction.

Tiede A, Eder M, von Depka M, Battmer K, Luther S, Kiem HP, Ganser A, Scherr M.

Gene Ther. 2003 Oct;10(22):1917-25.

PMID:
14502221
7.

Therapeutic factor VIII levels and negligible toxicity in mouse and dog models of hemophilia A following gene therapy with high-capacity adenoviral vectors.

Chuah MK, Schiedner G, Thorrez L, Brown B, Johnston M, Gillijns V, Hertel S, Van Rooijen N, Lillicrap D, Collen D, VandenDriessche T, Kochanek S.

Blood. 2003 Mar 1;101(5):1734-43. Epub 2002 Oct 24.

8.

Sustained expression of human factor VIII in mice using a parvovirus-based vector.

Chao H, Mao L, Bruce AT, Walsh CE.

Blood. 2000 Mar 1;95(5):1594-9.

9.

Heterogeneity of the immune response to adenovirus-mediated factor VIII gene therapy in different inbred hemophilic mouse strains.

Rawle FE, Shi CX, Brown B, McKinven A, Tinlin S, Graham FL, Hough C, Lillicrap D.

J Gene Med. 2004 Dec;6(12):1358-68.

PMID:
15493040
10.

Gene therapy for hemophilia A: production of therapeutic levels of human factor VIII in vivo in mice.

Dwarki VJ, Belloni P, Nijjar T, Smith J, Couto L, Rabier M, Clift S, Berns A, Cohen LK.

Proc Natl Acad Sci U S A. 1995 Feb 14;92(4):1023-7.

11.

[Genetic therapy for hemophiliacs--therapeutic potential and technological limits].

Michou AI, Christ M, Pavirani A, Mehtali M.

Transfus Clin Biol. 1997;4(3):251-61. Review. French.

PMID:
9264782
12.

High expression reduces an antibody response after neonatal gene therapy with B domain-deleted human factor VIII in mice.

Xu L, Mei M, Ma X, Ponder KP.

J Thromb Haemost. 2007 Sep;5(9):1805-12. Epub 2007 May 21.

13.

Sustained transgene expression by human cord blood derived CD34+ cells transduced with simian immunodeficiency virus agmTYO1-based vectors carrying the human coagulation factor VIII gene in NOD/SCID mice.

Kikuchi J, Mimuro J, Ogata K, Tabata T, Ueda Y, Ishiwata A, Kimura K, Takano K, Madoiwa S, Mizukami H, Hanazono Y, Kume A, Hasegawa M, Ozawa K, Sakata Y.

J Gene Med. 2004 Oct;6(10):1049-60. Erratum in: J Gene Med. 2005 Jun;7(6):836. Kimura, Konzoh [corrected to Kimura, Kouzoh].

PMID:
15386735
14.
15.

Expression of human coagulation factor VIII in adipocytes transduced with the simian immunodeficiency virus agmTYO1-based vector for hemophilia A gene therapy.

Ogata K, Mimuro J, Kikuchi J, Tabata T, Ueda Y, Naito M, Madoiwa S, Takano K, Hasegawa M, Ozawa K, Sakata Y.

Gene Ther. 2004 Feb;11(3):253-9.

PMID:
14737084
16.
17.

Sustained high-level expression of full-length human factor VIII and restoration of clotting activity in hemophilic mice using a minimal adenovirus vector.

Balagué C, Zhou J, Dai Y, Alemany R, Josephs SF, Andreason G, Hariharan M, Sethi E, Prokopenko E, Jan HY, Lou YC, Hubert-Leslie D, Ruiz L, Zhang WW.

Blood. 2000 Feb 1;95(3):820-8.

18.
19.

Induction of tolerance to human factor VIII in mice.

Chao H, Walsh CE.

Blood. 2001 May 15;97(10):3311-2.

20.

[Human factor VIII expression in retrovirus vector-transduced bone marrow stromal cells].

Guo X, Wang H, Chu H.

Zhonghua Xue Ye Xue Za Zhi. 2001 Sep;22(9):461-3. Chinese.

PMID:
11758224

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