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Items: 13

1.

Phagocytosis-shielded lentiviral vectors improve liver gene therapy in nonhuman primates.

Milani M, Annoni A, Moalli F, Liu T, Cesana D, Calabria A, Bartolaccini S, Biffi M, Russo F, Visigalli I, Raimondi A, Patarroyo-White S, Drager D, Cristofori P, Ayuso E, Montini E, Peters R, Iannacone M, Cantore A, Naldini L.

Sci Transl Med. 2019 May 22;11(493). pii: eaav7325. doi: 10.1126/scitranslmed.aav7325.

PMID:
31118293
2.

Preclinical Testing of the Safety and Tolerability of Lentiviral Vector-Mediated Above-Normal Alpha-L-Iduronidase Expression in Murine and Human Hematopoietic Cells Using Toxicology and Biodistribution Good Laboratory Practice Studies.

Visigalli I, Delai S, Ferro F, Cecere F, Vezzoli M, Sanvito F, Chanut F, Benedicenti F, Spinozzi G, Wynn R, Calabria A, Naldini L, Montini E, Cristofori P, Biffi A.

Hum Gene Ther. 2016 Oct;27(10):813-829. doi: 10.1089/hum.2016.068.

PMID:
27431943
3.

Maintenance of a functional hematopoietic stem cell niche through galactocerebrosidase and other enzymes.

Visigalli I, Biffi A.

Curr Opin Hematol. 2011 Jul;18(4):214-9. doi: 10.1097/MOH.0b013e3283477979. Review.

PMID:
21537167
4.

Identification of hematopoietic stem cell-specific miRNAs enables gene therapy of globoid cell leukodystrophy.

Gentner B, Visigalli I, Hiramatsu H, Lechman E, Ungari S, Giustacchini A, Schira G, Amendola M, Quattrini A, Martino S, Orlacchio A, Dick JE, Biffi A, Naldini L.

Sci Transl Med. 2010 Nov 17;2(58):58ra84. doi: 10.1126/scitranslmed.3001522.

5.

Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model.

Visigalli I, Delai S, Politi LS, Di Domenico C, Cerri F, Mrak E, D'Isa R, Ungaro D, Stok M, Sanvito F, Mariani E, Staszewsky L, Godi C, Russo I, Cecere F, Del Carro U, Rubinacci A, Brambilla R, Quattrini A, Di Natale P, Ponder K, Naldini L, Biffi A.

Blood. 2010 Dec 9;116(24):5130-9. doi: 10.1182/blood-2010-04-278234. Epub 2010 Sep 16.

6.

Sulfatase modifying factor 1-mediated fibroblast growth factor signaling primes hematopoietic multilineage development.

Buono M, Visigalli I, Bergamasco R, Biffi A, Cosma MP.

J Exp Med. 2010 Aug 2;207(8):1647-60. doi: 10.1084/jem.20091022. Epub 2010 Jul 19.

7.

The galactocerebrosidase enzyme contributes to the maintenance of a functional hematopoietic stem cell niche.

Visigalli I, Ungari S, Martino S, Park H, Cesani M, Gentner B, Sergi Sergi L, Orlacchio A, Naldini L, Biffi A.

Blood. 2010 Sep 16;116(11):1857-66. doi: 10.1182/blood-2009-12-256461. Epub 2010 May 28.

8.

Development and maturation of invariant NKT cells in the presence of lysosomal engulfment.

Plati T, Visigalli I, Capotondo A, Buono M, Naldini L, Cosma MP, Biffi A.

Eur J Immunol. 2009 Oct;39(10):2748-54. doi: 10.1002/eji.200939639.

9.

Dlg1, Sec8, and Mtmr2 regulate membrane homeostasis in Schwann cell myelination.

Bolis A, Coviello S, Visigalli I, Taveggia C, Bachi A, Chishti AH, Hanada T, Quattrini A, Previtali SC, Biffi A, Bolino A.

J Neurosci. 2009 Jul 8;29(27):8858-70. doi: 10.1523/JNEUROSCI.1423-09.2009.

10.

Monitoring disease evolution and treatment response in lysosomal disorders by the peripheral benzodiazepine receptor ligand PK11195.

Visigalli I, Moresco RM, Belloli S, Politi LS, Gritti A, Ungaro D, Matarrese M, Turolla E, Falini A, Scotti G, Naldini L, Fazio F, Biffi A.

Neurobiol Dis. 2009 Apr;34(1):51-62.

PMID:
19320046
11.

Specific determination of beta-galactocerebrosidase activity via competitive inhibition of beta-galactosidase.

Martino S, Tiribuzi R, Tortori A, Conti D, Visigalli I, Lattanzi A, Biffi A, Gritti A, Orlacchio A.

Clin Chem. 2009 Mar;55(3):541-8. doi: 10.1373/clinchem.2008.115873. Epub 2009 Jan 15.

12.

SUMF1 enhances sulfatase activities in vivo in five sulfatase deficiencies.

Fraldi A, Biffi A, Lombardi A, Visigalli I, Pepe S, Settembre C, Nusco E, Auricchio A, Naldini L, Ballabio A, Cosma MP.

Biochem J. 2007 Apr 15;403(2):305-12.

13.

Correction of metachromatic leukodystrophy in the mouse model by transplantation of genetically modified hematopoietic stem cells.

Biffi A, De Palma M, Quattrini A, Del Carro U, Amadio S, Visigalli I, Sessa M, Fasano S, Brambilla R, Marchesini S, Bordignon C, Naldini L.

J Clin Invest. 2004 Apr;113(8):1118-29.

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