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Items: 1 to 50 of 52

1.

Systemic AAV8-mediated delivery of a functional copy of muscle glycogen phosphorylase (Pygm) ameliorates disease in a murine model of McArdle disease.

McNamara EL, Taylor RL, Clayton JS, Goullee H, Dilworth KL, Pinós T, Brull A, Alexander IE, Lisowski L, Ravenscroft G, Laing NG, Nowak KJ.

Hum Mol Genet. 2019 Sep 12. pii: ddz214. doi: 10.1093/hmg/ddz214. [Epub ahead of print]

PMID:
31511858
2.

Objective assessment of visual acuity: a refined model for analyzing the sweep VEP.

Strasser T, Nasser F, Langrová H, Zobor D, Lisowski Ł, Hillerkuss D, Sailer C, Kurtenbach A, Zrenner E.

Doc Ophthalmol. 2019 Apr;138(2):97-116. doi: 10.1007/s10633-019-09672-z. Epub 2019 Jan 29.

PMID:
30694438
3.

Codon-Optimization of Wild-Type Adeno-Associated Virus Capsid Sequences Enhances DNA Family Shuffling while Conserving Functionality.

Cabanes-Creus M, Ginn SL, Amaya AK, Liao SHY, Westhaus A, Hallwirth CV, Wilmott P, Ward J, Dilworth KL, Santilli G, Rybicki A, Nakai H, Thrasher AJ, Filip AC, Alexander IE, Lisowski L.

Mol Ther Methods Clin Dev. 2018 Nov 1;12:71-84. doi: 10.1016/j.omtm.2018.10.016. eCollection 2019 Mar 15.

4.

Directed Evolution of Adeno-Associated Virus Vectors in Human Cardiomyocytes for Cardiac Gene Therapy.

Kok CY, Alexander I, Lisowski L, Kizana E.

Heart Lung Circ. 2018 Nov;27(11):1270-1273. doi: 10.1016/j.hlc.2018.08.014. No abstract available.

PMID:
30274736
5.

An Atypical Parvovirus Drives Chronic Tubulointerstitial Nephropathy and Kidney Fibrosis.

Roediger B, Lee Q, Tikoo S, Cobbin JCA, Henderson JM, Jormakka M, O'Rourke MB, Padula MP, Pinello N, Henry M, Wynne M, Santagostino SF, Brayton CF, Rasmussen L, Lisowski L, Tay SS, Harris DC, Bertram JF, Dowling JP, Bertolino P, Lai JH, Wu W, Bachovchin WW, Wong JJ, Gorrell MD, Shaban B, Holmes EC, Jolly CJ, Monette S, Weninger W.

Cell. 2018 Oct 4;175(2):530-543.e24. doi: 10.1016/j.cell.2018.08.013. Epub 2018 Sep 13.

6.

Optogenetic approaches to vision restoration.

Simunovic MP, Shen W, Lin JY, Protti DA, Lisowski L, Gillies MC.

Exp Eye Res. 2019 Jan;178:15-26. doi: 10.1016/j.exer.2018.09.003. Epub 2018 Sep 13. Review.

PMID:
30218651
7.

Bioengineered Viral Platform for Intramuscular Passive Vaccine Delivery to Human Skeletal Muscle.

Paulk NK, Pekrun K, Charville GW, Maguire-Nguyen K, Wosczyna MN, Xu J, Zhang Y, Lisowski L, Yoo B, Vilches-Moure JG, Lee GK, Shrager JB, Rando TA, Kay MA.

Mol Ther Methods Clin Dev. 2018 Jul 24;10:144-155. doi: 10.1016/j.omtm.2018.06.001. eCollection 2018 Sep 21.

8.

Age-Related Seroprevalence of Antibodies Against AAV-LK03 in a UK Population Cohort.

Perocheau DP, Cunningham S, Lee J, Antinao Diaz J, Waddington SN, Gilmour K, Eaglestone S, Lisowski L, Thrasher AJ, Alexander IE, Gissen P, Baruteau J.

Hum Gene Ther. 2019 Jan;30(1):79-87. doi: 10.1089/hum.2018.098. Epub 2018 Oct 19.

9.

In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation.

Moreno AM, Fu X, Zhu J, Katrekar D, Shih YV, Marlett J, Cabotaje J, Tat J, Naughton J, Lisowski L, Varghese S, Zhang K, Mali P.

Mol Ther. 2018 Jul 5;26(7):1818-1827. doi: 10.1016/j.ymthe.2018.04.017. Epub 2018 Apr 25.

10.

Multiplexed in vivo homology-directed repair and tumor barcoding enables parallel quantification of Kras variant oncogenicity.

Winters IP, Chiou SH, Paulk NK, McFarland CD, Lalgudi PV, Ma RK, Lisowski L, Connolly AJ, Petrov DA, Kay MA, Winslow MM.

Nat Commun. 2017 Dec 12;8(1):2053. doi: 10.1038/s41467-017-01519-y.

11.

Bioengineered AAV Capsids with Combined High Human Liver Transduction In Vivo and Unique Humoral Seroreactivity.

Paulk NK, Pekrun K, Zhu E, Nygaard S, Li B, Xu J, Chu K, Leborgne C, Dane AP, Haft A, Zhang Y, Zhang F, Morton C, Valentine MB, Davidoff AM, Nathwani AC, Mingozzi F, Grompe M, Alexander IE, Lisowski L, Kay MA.

Mol Ther. 2018 Jan 3;26(1):289-303. doi: 10.1016/j.ymthe.2017.09.021. Epub 2017 Sep 25.

12.

Identification of liver-specific enhancer-promoter activity in the 3' untranslated region of the wild-type AAV2 genome.

Logan GJ, Dane AP, Hallwirth CV, Smyth CM, Wilkie EE, Amaya AK, Zhu E, Khandekar N, Ginn SL, Liao SHY, Cunningham SC, Sasaki N, Cabanes-Creus M, Tam PPL, Russell DW, Lisowski L, Alexander IE.

Nat Genet. 2017 Aug;49(8):1267-1273. doi: 10.1038/ng.3893. Epub 2017 Jun 19.

PMID:
28628105
13.

Development of a Chromatic Pupillography Protocol for the First Gene Therapy Trial in Patients With CNGA3-Linked Achromatopsia.

Lisowska J, Lisowski L, Kelbsch C, Maeda F, Richter P, Kohl S, Zobor D, Strasser T, Stingl K, Zrenner E, Peters T, Wilhelm H, Fischer MD, Wilhelm B; RD-CURE Consortium.

Invest Ophthalmol Vis Sci. 2017 Feb 1;58(2):1274-1282. doi: 10.1167/iovs.16-20505.

PMID:
28241315
14.

Ten- to 15-year results of the Oxford Phase III mobile unicompartmental knee arthroplasty: a prospective study from a non-designer group.

Lisowski LA, Meijer LI, van den Bekerom MP, Pilot P, Lisowski AE.

Bone Joint J. 2016 Oct;98 B(10 Supple B):41-47.

15.

Analysis of retinal function using chromatic pupillography in retinitis pigmentosa and the relationship to electrically evoked phosphene thresholds.

Kelbsch C, Maeda F, Lisowska J, Lisowski L, Strasser T, Stingl K, Wilhelm B, Wilhelm H, Peters T.

Acta Ophthalmol. 2017 Jun;95(4):e261-e269. doi: 10.1111/aos.13259. Epub 2016 Sep 29.

16.

RNA interference-induced hepatotoxicity results from loss of the first synthesized isoform of microRNA-122 in mice.

Valdmanis PN, Gu S, Chu K, Jin L, Zhang F, Munding EM, Zhang Y, Huang Y, Kutay H, Ghoshal K, Lisowski L, Kay MA.

Nat Med. 2016 May;22(5):557-62. doi: 10.1038/nm.4079. Epub 2016 Apr 11.

17.

Adeno-associated virus serotypes for gene therapeutics.

Lisowski L, Tay SS, Alexander IE.

Curr Opin Pharmacol. 2015 Oct;24:59-67. doi: 10.1016/j.coph.2015.07.006. Epub 2015 Aug 25. Review.

PMID:
26291407
18.

Human COL7A1-corrected induced pluripotent stem cells for the treatment of recessive dystrophic epidermolysis bullosa.

Sebastiano V, Zhen HH, Haddad B, Bashkirova E, Melo SP, Wang P, Leung TL, Siprashvili Z, Tichy A, Li J, Ameen M, Hawkins J, Lee S, Li L, Schwertschkow A, Bauer G, Lisowski L, Kay MA, Kim SK, Lane AT, Wernig M, Oro AE.

Sci Transl Med. 2014 Nov 26;6(264):264ra163. doi: 10.1126/scitranslmed.3009540. Erratum in: Sci Transl Med. 2014 Dec 17;6(267):267er8. Derafshi, Bahareh Haddad [corrected to Haddad, Bahareh].

19.

Genome editing of isogenic human induced pluripotent stem cells recapitulates long QT phenotype for drug testing.

Wang Y, Liang P, Lan F, Wu H, Lisowski L, Gu M, Hu S, Kay MA, Urnov FD, Shinnawi R, Gold JD, Gepstein L, Wu JC.

J Am Coll Cardiol. 2014 Aug 5;64(5):451-9. doi: 10.1016/j.jacc.2014.04.057.

20.

Second generation codon optimized minicircle (CoMiC) for nonviral reprogramming of human adult fibroblasts.

Diecke S, Lisowski L, Kooreman NG, Wu JC.

Methods Mol Biol. 2014;1181:1-13. doi: 10.1007/978-1-4939-1047-2_1.

21.

Selection and evaluation of clinically relevant AAV variants in a xenograft liver model.

Lisowski L, Dane AP, Chu K, Zhang Y, Cunningham SC, Wilson EM, Nygaard S, Grompe M, Alexander IE, Kay MA.

Nature. 2014 Feb 20;506(7488):382-6. doi: 10.1038/nature12875. Epub 2013 Dec 25.

22.

Somatic correction of junctional epidermolysis bullosa by a highly recombinogenic AAV variant.

Melo SP, Lisowski L, Bashkirova E, Zhen HH, Chu K, Keene DR, Marinkovich MP, Kay MA, Oro AE.

Mol Ther. 2014 Apr;22(4):725-33. doi: 10.1038/mt.2013.290. Epub 2014 Jan 6.

23.

Plasma levels of IL-17, VEGF, and adrenomedullin and S-cone dysfunction of the retina in children and adolescents without signs of retinopathy and with varied duration of diabetes.

Semeran K, Pawłowski P, Lisowski Ł, Szczepaniak I, Wójtowicz J, Ławicki S, Bakunowicz-Łazarczyk A, Bossowski A.

Mediators Inflamm. 2013;2013:274726. doi: 10.1155/2013/274726. Epub 2013 Nov 18.

24.

Comparison of transduction efficiency among various lentiviruses containing GFP reporter in bone marrow hematopoietic stem cell transplantation.

Wang N, Rajasekaran N, Hou T, Lisowski L, Mellins ED.

Exp Hematol. 2013 Nov;41(11):934-43. doi: 10.1016/j.exphem.2013.07.002. Epub 2013 Aug 14.

25.

The anti-genomic (negative) strand of Hepatitis C Virus is not targetable by shRNA.

Lisowski L, Elazar M, Chu K, Glenn JS, Kay MA.

Nucleic Acids Res. 2013 Apr 1;41(6):3688-98. doi: 10.1093/nar/gkt068. Epub 2013 Feb 8.

26.

rAAV-mediated tumorigenesis: still unresolved after an AAV assault.

Valdmanis PN, Lisowski L, Kay MA.

Mol Ther. 2012 Nov;20(11):2014-7. doi: 10.1038/mt.2012.220. No abstract available.

27.

AAV vectors containing rDNA homology display increased chromosomal integration and transgene persistence.

Wang Z, Lisowski L, Finegold MJ, Nakai H, Kay MA, Grompe M.

Mol Ther. 2012 Oct;20(10):1902-11. doi: 10.1038/mt.2012.157. Epub 2012 Sep 18.

28.

Ribosomal DNA integrating rAAV-rDNA vectors allow for stable transgene expression.

Lisowski L, Lau A, Wang Z, Zhang Y, Zhang F, Grompe M, Kay MA.

Mol Ther. 2012 Oct;20(10):1912-23. doi: 10.1038/mt.2012.164. Epub 2012 Sep 18.

29.

Genome editing of human embryonic stem cells and induced pluripotent stem cells with zinc finger nucleases for cellular imaging.

Wang Y, Zhang WY, Hu S, Lan F, Lee AS, Huber B, Lisowski L, Liang P, Huang M, de Almeida PE, Won JH, Sun N, Robbins RC, Kay MA, Urnov FD, Wu JC.

Circ Res. 2012 Dec 7;111(12):1494-503. doi: 10.1161/CIRCRESAHA.112.274969. Epub 2012 Sep 11.

30.

Tuberositas osteotomy for total knee arthroplasty: a review of the literature.

Zonnenberg CB, Lisowski LA, van den Bekerom MP, Nolte PA.

J Knee Surg. 2010 Sep;23(3):121-9. Review.

PMID:
21329253
31.

Oxford Phase 3 unicompartmental knee arthroplasty: medium-term results of a minimally invasive surgical procedure.

Lisowski LA, van den Bekerom MP, Pilot P, van Dijk CN, Lisowski AE.

Knee Surg Sports Traumatol Arthrosc. 2011 Feb;19(2):277-84. doi: 10.1007/s00167-010-1213-2. Epub 2010 Jul 17.

32.

Preoperative acidosis and infant development following surgery for congenital heart disease.

Verheijen PM, Lisowski LA, Wassink S, Visser GH, Meijboom EJ.

Herz. 2010 Aug;35(5):358-63. doi: 10.1007/s00059-010-3356-9. Epub 2010 Jul 15.

PMID:
20628709
33.

Congenital heart disease in pregnancies complicated by maternal diabetes mellitus. An international clinical collaboration, literature review, and meta-analysis.

Lisowski LA, Verheijen PM, Copel JA, Kleinman CS, Wassink S, Visser GH, Meijboom EJ.

Herz. 2010 Jan;35(1):19-26. doi: 10.1007/s00059-010-3244-3. Epub 2010 Feb 9. Review.

PMID:
20140785
34.

Traumatic recurrent distal radioulnar joint dislocation: a case report.

Wassink S, Lisowski LA, Schutte BG.

Strategies Trauma Limb Reconstr. 2009 Dec;4(3):141-3. doi: 10.1007/s11751-009-0073-0. Epub 2009 Nov 24.

35.

Supplying clotting factors from hematopoietic stem cell-derived erythroid and megakaryocytic lineage cells.

Sadelain M, Chang A, Lisowski L.

Mol Ther. 2009 Dec;17(12):1994-9. doi: 10.1038/mt.2009.238. Epub 2009 Oct 20. Review.

36.

Transient in vivo beta-globin production after lentiviral gene transfer to hematopoietic stem cells in the nonhuman primate.

Hayakawa J, Ueda T, Lisowski L, Hsieh MM, Washington K, Phang O, Metzger M, Krouse A, Donahue RE, Sadelain M, Tisdale JF.

Hum Gene Ther. 2009 Jun;20(6):563-72. doi: 10.1089/hum.2008.186.

37.

Metastatic malignant peripheral nerve sheath tumor in a newborn.

Lisowski LA, Bramer JA, de Jonge MC, Bras J, Van der Horst CM, de Kraker J.

J Pediatr Hematol Oncol. 2008 Dec;30(12):891-5. doi: 10.1097/MPH.0b013e31818b3572.

PMID:
19131773
38.

Erythroid-specific human factor IX delivery from in vivo selected hematopoietic stem cells following nonmyeloablative conditioning in hemophilia B mice.

Chang AH, Stephan MT, Lisowski L, Sadelain M.

Mol Ther. 2008 Oct;16(10):1745-52. doi: 10.1038/mt.2008.161. Epub 2008 Aug 5.

39.

Current status of globin gene therapy for the treatment of beta-thalassaemia.

Lisowski L, Sadelain M.

Br J Haematol. 2008 May;141(3):335-45. doi: 10.1111/j.1365-2141.2008.07098.x. Review.

PMID:
18410569
40.
41.

Oxford Phase 3 Unicompartmental Knee Arthroplasty (UKA): Clinical and radiological results of minimum follow-up of 2 years.

Lisowski LA, Verheijen PM, Lisowski AE.

Ortop Traumatol Rehabil. 2004 Nov-Dec;6(6):773-6.

42.

Functional improvement after unicompartmental knee replacement: a follow-up study with a performance based knee test.

Kleijn LL, van Hemert WL, Meijers WG, Kester AD, Lisowski L, Grimm B, Heyligers IC.

Knee Surg Sports Traumatol Arthrosc. 2007 Oct;15(10):1187-93. Epub 2007 Jun 23.

PMID:
17589828
43.

Endothelial-cardiomyocyte interactions in cardiac development and repair.

Hsieh PC, Davis ME, Lisowski LK, Lee RT.

Annu Rev Physiol. 2006;68:51-66. Review.

44.

A genetic strategy to treat sickle cell anemia by coregulating globin transgene expression and RNA interference.

Samakoglu S, Lisowski L, Budak-Alpdogan T, Usachenko Y, Acuto S, Di Marzo R, Maggio A, Zhu P, Tisdale JF, Rivière I, Sadelain M.

Nat Biotechnol. 2006 Jan;24(1):89-94. Epub 2005 Dec 25.

PMID:
16378095
45.

Progress toward the genetic treatment of the beta-thalassemias.

Sadelain M, Lisowski L, Samakoglu S, Rivella S, May C, Riviere I.

Ann N Y Acad Sci. 2005;1054:78-91. Review.

PMID:
16339654
46.

Globin gene transfer for treatment of the beta-thalassemias and sickle cell disease.

Sadelain M, Rivella S, Lisowski L, Samakoglu S, Rivière I.

Best Pract Res Clin Haematol. 2004 Sep;17(3):517-34. Review.

PMID:
15498721
47.

Prenatal diagnosis of the fetus with hypoplastic left heart syndrome management and outcome.

Verheijen PM, Lisowski LA, Plantinga RF, Hitchcock JF, Bennink GB, Stoutenbeek P, Meijboom EJ.

Herz. 2003 May;28(3):250-6.

PMID:
12756482
48.

Altered fetal circulation in type-1 diabetic pregnancies.

Lisowski LA, Verheijen PM, De Smedt MM, Visser GH, Meijboom EJ.

Ultrasound Obstet Gynecol. 2003 Apr;21(4):365-9. Erratum in: Ultrasound Obstet Gynecol. 2003 Jul;22(1):iv.

49.

[Correlation between prenatal ultrasound diagnosis and findings from autopsies or neonatal operations due to structural congenital heart defects; a retrospective analysis].

Verheijen PM, Michon MM, Lisowski LA, Oudijk MA, Stoutenbeek P, Meijboom EJ.

Ned Tijdschr Geneeskd. 2002 Nov 30;146(48):2297-302. Dutch.

PMID:
12497759
50.

Lactacidosis in the neonate is minimized by prenatal detection of congenital heart disease.

Verheijen PM, Lisowski LA, Stoutenbeek P, Hitchcock JF, Bennink GB, Meijboom EJ.

Ultrasound Obstet Gynecol. 2002 Jun;19(6):552-5.

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