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Items: 44

1.

Influence of Pre-existing Anti-capsid Neutralizing and Binding Antibodies on AAV Vector Transduction.

Fitzpatrick Z, Leborgne C, Barbon E, Masat E, Ronzitti G, van Wittenberghe L, Vignaud A, Collaud F, Charles S, Simon Sola M, Jouen F, Boyer O, Mingozzi F.

Mol Ther Methods Clin Dev. 2018 Feb 13;9:119-129. doi: 10.1016/j.omtm.2018.02.003. eCollection 2018 Jun 15.

2.

Prevalence and long-term monitoring of humoral immunity against adeno-associated virus in Duchenne Muscular Dystrophy patients.

Leborgne C, Latournerie V, Boutin S, Desgue D, Quéré A, Pignot E, Collaud F, Charles S, Simon Sola M, Masat E, Jouen F, Boyer O, Masurier C, Mingozzi F, Veron P.

Cell Immunol. 2018 Mar 16. pii: S0008-8749(18)30114-X. doi: 10.1016/j.cellimm.2018.03.004. [Epub ahead of print]

PMID:
29571923
3.

Enhanced liver gene transfer and evasion of preexisting humoral immunity with exosome-enveloped AAV vectors.

Meliani A, Boisgerault F, Fitzpatrick Z, Marmier S, Leborgne C, Collaud F, Simon Sola M, Charles S, Ronzitti G, Vignaud A, van Wittenberghe L, Marolleau B, Jouen F, Tan S, Boyer O, Christophe O, Brisson AR, Maguire CA, Mingozzi F.

Blood Adv. 2017 Oct 16;1(23):2019-2031. doi: 10.1182/bloodadvances.2017010181. eCollection 2017 Oct 24.

4.

Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase.

Puzzo F, Colella P, Biferi MG, Bali D, Paulk NK, Vidal P, Collaud F, Simon-Sola M, Charles S, Hardet R, Leborgne C, Meliani A, Cohen-Tannoudji M, Astord S, Gjata B, Sellier P, van Wittenberghe L, Vignaud A, Boisgerault F, Barkats M, Laforet P, Kay MA, Koeberl DD, Ronzitti G, Mingozzi F.

Sci Transl Med. 2017 Nov 29;9(418). pii: eaam6375. doi: 10.1126/scitranslmed.aam6375.

5.

Bioengineered AAV Capsids with Combined High Human Liver Transduction In Vivo and Unique Humoral Seroreactivity.

Paulk NK, Pekrun K, Zhu E, Nygaard S, Li B, Xu J, Chu K, Leborgne C, Dane AP, Haft A, Zhang Y, Zhang F, Morton C, Valentine MB, Davidoff AM, Nathwani AC, Mingozzi F, Grompe M, Alexander IE, Lisowski L, Kay MA.

Mol Ther. 2018 Jan 3;26(1):289-303. doi: 10.1016/j.ymthe.2017.09.021. Epub 2017 Sep 25.

PMID:
29055620
6.

Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction.

Han SO, Ronzitti G, Arnson B, Leborgne C, Li S, Mingozzi F, Koeberl D.

Mol Ther Methods Clin Dev. 2017 Jan 11;4:126-136. doi: 10.1016/j.omtm.2016.12.010. eCollection 2017 Mar 17.

7.

The absorption enhancer sodium deoxycholate promotes high gene transfer in skeletal muscles.

Leborgne C, Alimi-Guez D, El Shafey N, van Wittenberghe L, Bigey P, Scherman D, Kichler A.

Int J Pharm. 2017 May 15;523(1):291-299. doi: 10.1016/j.ijpharm.2017.03.020. Epub 2017 Mar 14.

PMID:
28315384
8.

Histidine-rich designer peptides of the LAH4 family promote cell delivery of a multitude of cargo.

Moulay G, Leborgne C, Mason AJ, Aisenbrey C, Kichler A, Bechinger B.

J Pept Sci. 2017 Apr;23(4):320-328. doi: 10.1002/psc.2955. Epub 2017 Jan 9.

PMID:
28067008
9.

A translationally optimized AAV-UGT1A1 vector drives safe and long-lasting correction of Crigler-Najjar syndrome.

Ronzitti G, Bortolussi G, van Dijk R, Collaud F, Charles S, Leborgne C, Vidal P, Martin S, Gjata B, Sola MS, van Wittenberghe L, Vignaud A, Veron P, Bosma PJ, Muro AF, Mingozzi F.

Mol Ther Methods Clin Dev. 2016 Jul 20;3:16049. eCollection 2016.

10.

Determination of anti-adeno-associated virus vector neutralizing antibody titer with an in vitro reporter system.

Meliani A, Leborgne C, Triffault S, Jeanson-Leh L, Veron P, Mingozzi F.

Hum Gene Ther Methods. 2015 Apr;26(2):45-53. doi: 10.1089/hgtb.2015.037.

11.

Biochemical, histological and functional correction of mucopolysaccharidosis type IIIB by intra-cerebrospinal fluid gene therapy.

Ribera A, Haurigot V, Garcia M, Marcó S, Motas S, Villacampa P, Maggioni L, León X, Molas M, Sánchez V, Muñoz S, Leborgne C, Moll X, Pumarola M, Mingozzi F, Ruberte J, Añor S, Bosch F.

Hum Mol Genet. 2015 Apr 1;24(7):2078-95. doi: 10.1093/hmg/ddu727. Epub 2014 Dec 18.

PMID:
25524704
12.

Enhanced efficacy from gene therapy in Pompe disease using coreceptor blockade.

Han SO, Li S, Brooks ED, Masat E, Leborgne C, Banugaria S, Bird A, Mingozzi F, Waldmann H, Koeberl D.

Hum Gene Ther. 2015 Jan;26(1):26-35. doi: 10.1089/hum.2014.115.

13.

Forelimb treatment in a large cohort of dystrophic dogs supports delivery of a recombinant AAV for exon skipping in Duchenne patients.

Le Guiner C, Montus M, Servais L, Cherel Y, Francois V, Thibaud JL, Wary C, Matot B, Larcher T, Guigand L, Dutilleul M, Domenger C, Allais M, Beuvin M, Moraux A, Le Duff J, Devaux M, Jaulin N, Guilbaud M, Latournerie V, Veron P, Boutin S, Leborgne C, Desgue D, Deschamps JY, Moullec S, Fromes Y, Vulin A, Smith RH, Laroudie N, Barnay-Toutain F, Rivière C, Bucher S, Le TH, Delaunay N, Gasmi M, Kotin RM, Bonne G, Adjali O, Masurier C, Hogrel JY, Carlier P, Moullier P, Voit T.

Mol Ther. 2014 Nov;22(11):1923-35. doi: 10.1038/mt.2014.151. Epub 2014 Aug 4.

14.

N-3 fatty acid enriched eggs and production of egg yolk powders: an increased risk of lipid oxidation?

Meynier A, Leborgne C, Viau M, Schuck P, Guichardant M, Rannou C, Anton M.

Food Chem. 2014 Jun 15;153:94-100. doi: 10.1016/j.foodchem.2013.12.028. Epub 2013 Dec 11.

PMID:
24491705
15.

Humoral and cellular capsid-specific immune responses to adeno-associated virus type 1 in randomized healthy donors.

Veron P, Leborgne C, Monteilhet V, Boutin S, Martin S, Moullier P, Masurier C.

J Immunol. 2012 Jun 15;188(12):6418-24. doi: 10.4049/jimmunol.1200620. Epub 2012 May 16.

16.

Smart DNA vectors based on cyclodextrin polymers: compaction and endosomal release.

Wintgens V, Leborgne C, Baconnais S, Burckbuchler V, Le Cam E, Scherman D, Kichler A, Amiel C.

Pharm Res. 2012 Feb;29(2):384-96. doi: 10.1007/s11095-011-0560-0. Epub 2011 Aug 17.

PMID:
21847694
17.

A 10 patient case report on the impact of plasmapheresis upon neutralizing factors against adeno-associated virus (AAV) types 1, 2, 6, and 8.

Monteilhet V, Saheb S, Boutin S, Leborgne C, Veron P, Montus MF, Moullier P, Benveniste O, Masurier C.

Mol Ther. 2011 Nov;19(11):2084-91. doi: 10.1038/mt.2011.108. Epub 2011 May 31.

18.

Synthesis of poly(propylene glycol)-block-polyethylenimine triblock copolymers for the delivery of nucleic acids.

Brissault B, Leborgne C, Scherman D, Guis C, Kichler A.

Macromol Biosci. 2011 May 12;11(5):652-61. doi: 10.1002/mabi.201000404. Epub 2011 Feb 8.

PMID:
21305695
19.

Investigation of DNA condensing properties of amphiphilic triblock cationic polymers by atomic force microscopy.

Lidgi-Guigui N, Guis C, Brissault B, Kichler A, Leborgne C, Scherman D, Labdi S, Curmi PA.

Langmuir. 2010 Nov 16;26(22):17552-7. doi: 10.1021/la103066c. Epub 2010 Oct 7.

PMID:
20929211
20.

Incorporation of 2,3-diaminopropionic acid into linear cationic amphipathic peptides produces pH-sensitive vectors.

Lan Y, Langlet-Bertin B, Abbate V, Vermeer LS, Kong X, Sullivan KE, Leborgne C, Scherman D, Hider RC, Drake AF, Bansal SS, Kichler A, Mason AJ.

Chembiochem. 2010 Jun 14;11(9):1266-72. doi: 10.1002/cbic.201000073.

21.

Design and evaluation of histidine-rich amphipathic peptides for siRNA delivery.

Langlet-Bertin B, Leborgne C, Scherman D, Bechinger B, Mason AJ, Kichler A.

Pharm Res. 2010 Jul;27(7):1426-36. doi: 10.1007/s11095-010-0138-2.

PMID:
20393870
22.

Nucleic acid transfer with hemifluorinated polycationic lipids.

Klein E, Leborgne C, Ciobanu M, Klein J, Frisch B, Pons F, Zuber G, Scherman D, Kichler A, Lebeau L.

Biomaterials. 2010 Jun;31(17):4781-8. doi: 10.1016/j.biomaterials.2010.02.047. Epub 2010 Mar 29.

PMID:
20303166
23.

"HFP" fluorinated cationic lipids for enhanced lipoplex stability and gene delivery.

Klein E, Ciobanu M, Klein J, Machi V, Leborgne C, Vandamme T, Frisch B, Pons F, Kichler A, Zuber G, Lebeau L.

Bioconjug Chem. 2010 Feb 17;21(2):360-71. doi: 10.1021/bc900469z.

PMID:
20099841
24.

Prevalence of serum IgG and neutralizing factors against adeno-associated virus (AAV) types 1, 2, 5, 6, 8, and 9 in the healthy population: implications for gene therapy using AAV vectors.

Boutin S, Monteilhet V, Veron P, Leborgne C, Benveniste O, Montus MF, Masurier C.

Hum Gene Ther. 2010 Jun;21(6):704-12. doi: 10.1089/hum.2009.182.

PMID:
20095819
25.

Evaluation of the muscle gene transfer activity of a series of amphiphilic triblock copolymers.

Alimi-Guez D, Leborgne C, Pembouong G, Van Wittenberghe L, Mignet N, Scherman D, Kichler A.

J Gene Med. 2009 Dec;11(12):1114-24. doi: 10.1002/jgm.1396.

PMID:
19757455
26.

Development and characterization of new cyclodextrin polymer-based DNA delivery systems.

Burckbuchler V, Wintgens V, Leborgne C, Lecomte S, Leygue N, Scherman D, Kichler A, Amiel C.

Bioconjug Chem. 2008 Dec;19(12):2311-20. doi: 10.1021/bc800070f.

PMID:
19053313
27.

Synthesis and evaluation of amphiphilic poly(tetrahydrofuran-b-ethylene oxide) copolymers for DNA delivery into skeletal muscle.

Pomel C, Leborgne C, Cheradame H, Scherman D, Kichler A, Guegan P.

Pharm Res. 2008 Dec;25(12):2963-71. doi: 10.1007/s11095-008-9698-9. Epub 2008 Sep 3.

PMID:
18769873
28.

Self-promoted cellular uptake of peptide/DNA transfection complexes.

Prongidi-Fix L, Sugawara M, Bertani P, Raya J, Leborgne C, Kichler A, Bechinger B.

Biochemistry. 2007 Oct 9;46(40):11253-62. Epub 2007 Sep 12.

PMID:
17848098
29.

Amphiphilic poly[(propylene glycol)-block-(2-methyl-2-oxazoline)] copolymers for gene transfer in skeletal muscle.

Brissault B, Kichler A, Leborgne C, Jarroux N, Cheradame H, Guis C.

ChemMedChem. 2007 Aug;2(8):1202-7.

PMID:
17607797
30.

Optimising histidine rich peptides for efficient DNA delivery in the presence of serum.

Mason AJ, Leborgne C, Moulay G, Martinez A, Danos O, Bechinger B, Kichler A.

J Control Release. 2007 Mar 12;118(1):95-104. Epub 2006 Dec 8.

PMID:
17254661
31.

Characterization of the gene transfer process mediated by histidine-rich peptides.

Kichler A, Leborgne C, Danos O, Bechinger B.

J Mol Med (Berl). 2007 Feb;85(2):191-201. Epub 2006 Nov 17.

PMID:
17111132
32.

Synthesis, characterization, and gene transfer application of poly(ethylene glycol-b-ethylenimine) with high molar mass polyamine block.

Brissault B, Kichler A, Leborgne C, Danos O, Cheradame H, Gau J, Auvray L, Guis C.

Biomacromolecules. 2006 Oct;7(10):2863-70.

PMID:
17025363
33.

Linear topology confers in vivo gene transfer activity to polyethylenimines.

Brissault B, Leborgne C, Guis C, Danos O, Cheradame H, Kichler A.

Bioconjug Chem. 2006 May-Jun;17(3):759-65.

PMID:
16704215
34.

DNA compaction into new DNA vectors based on cyclodextrin polymer: surface enhanced Raman spectroscopy characterization.

Burckbuchler V, Wintgens V, Lecomte S, Percot A, Leborgne C, Danos O, Kichler A, Amiel C.

Biopolymers. 2006 Apr 5;81(5):360-70.

PMID:
16358247
35.

Cationic steroid antibiotics demonstrate DNA delivery properties.

Kichler A, Leborgne C, Savage PB, Danos O.

J Control Release. 2005 Sep 20;107(1):174-82.

PMID:
16126297
36.

Dilution of reporter gene with stuffer DNA does not alter the transfection efficiency of polyethylenimines.

Kichler A, Leborgne C, Danos O.

J Gene Med. 2005 Nov;7(11):1459-67.

PMID:
16041686
37.

Preparation and evaluation of a new class of gene transfer reagents: poly(-alkylaminosiloxanes).

Kichler A, Sabourault N, Décor R, Leborgne C, Schmutz M, Valleix A, Danos O, Wagner A, Mioskowski C.

J Control Release. 2003 Dec 12;93(3):403-14.

PMID:
14644589
38.

Synthesis of linear polyethylenimine derivatives for DNA transfection.

Brissault B, Kichler A, Guis C, Leborgne C, Danos O, Cheradame H.

Bioconjug Chem. 2003 May-Jun;14(3):581-7.

PMID:
12757382
39.

Histidine-rich amphipathic peptide antibiotics promote efficient delivery of DNA into mammalian cells.

Kichler A, Leborgne C, März J, Danos O, Bechinger B.

Proc Natl Acad Sci U S A. 2003 Feb 18;100(4):1564-8. Epub 2003 Jan 31.

40.

Intranasal gene delivery with a polyethylenimine-PEG conjugate.

Kichler A, Chillon M, Leborgne C, Danos O, Frisch B.

J Control Release. 2002 Jun 17;81(3):379-88.

PMID:
12044576
41.

Polyethylenimine-mediated gene delivery: a mechanistic study.

Kichler A, Leborgne C, Coeytaux E, Danos O.

J Gene Med. 2001 Mar-Apr;3(2):135-44.

PMID:
11318112
42.

Efficient DNA transfection mediated by the C-terminal domain of human immunodeficiency virus type 1 viral protein R.

Kichler A, Pages JC, Leborgne C, Druillennec S, Lenoir C, Coulaud D, Delain E, Le Cam E, Roques BP, Danos O.

J Virol. 2000 Jun;74(12):5424-31. Erratum in: J Virol. 2000 Dec;74(24):12003.

43.

Carcase characteristics of a heavy Japanese quail line under introgression with the roux gene.

Minvielle E, Gandemer G, Maeda Y, Leborgne C, Hirigoyen E, Boulay M.

Br Poult Sci. 2000 Mar;41(1):41-5.

PMID:
10821521
44.

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