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Items: 1 to 20 of 53


Intrathecal Adeno-Associated Virus Vector-mediated Gene Delivery for Adrenomyeloneuropathy.

Gong Y, Berenson A, Laheji F, Gao G, Wang D, Ng C, Volak A, Kok R, Kreouzis V, Dijkstra I, Kemp S, Maguire CA, Eichler F.

Hum Gene Ther. 2018 Oct 25. doi: 10.1089/hum.2018.079. [Epub ahead of print]


Treatment burden should be included in clinical practice guidelines.

Dobler CC, Harb N, Maguire CA, Armour CL, Coleman C, Murad MH.

BMJ. 2018 Oct 12;363:k4065. doi: 10.1136/bmj.k4065. No abstract available.


Efficient Gene Transfer to the Central Nervous System by Single-Stranded Anc80L65.

Hudry E, Andres-Mateos E, Lerner EP, Volak A, Cohen O, Hyman BT, Maguire CA, Vandenberghe LH.

Mol Ther Methods Clin Dev. 2018 Jul 23;10:197-209. doi: 10.1016/j.omtm.2018.07.006. eCollection 2018 Sep 21.


PACAP neurons in the ventral premammillary nucleus regulate reproductive function in the female mouse.

Ross RA, Leon S, Madara JC, Schafer D, Fergani C, Maguire CA, Verstegen AM, Brengle E, Kong D, Herbison AE, Kaiser UB, Lowell BB, Navarro VM.

Elife. 2018 Jun 15;7. pii: e35960. doi: 10.7554/eLife.35960.


CRISPR/Cas9 Mediated Disruption of the Swedish APP Allele as a Therapeutic Approach for Early-Onset Alzheimer's Disease.

György B, Lööv C, Zaborowski MP, Takeda S, Kleinstiver BP, Commins C, Kastanenka K, Mu D, Volak A, Giedraitis V, Lannfelt L, Maguire CA, Joung JK, Hyman BT, Breakefield XO, Ingelsson M.

Mol Ther Nucleic Acids. 2018 Jun 1;11:429-440. doi: 10.1016/j.omtn.2018.03.007. Epub 2018 Mar 16.


Virus vector-mediated genetic modification of brain tumor stromal cells after intravenous delivery.

Volak A, LeRoy SG, Natasan JS, Park DJ, Cheah PS, Maus A, Fitzpatrick Z, Hudry E, Pinkham K, Gandhi S, Hyman BT, Mu D, GuhaSarkar D, Stemmer-Rachamimov AO, Sena-Esteves M, Badr CE, Maguire CA.

J Neurooncol. 2018 May 16. doi: 10.1007/s11060-018-2889-2. [Epub ahead of print]


A melanocytic cuckoo.

Maguire CA, Elliot V, Pees B, Rosen A.

JAAD Case Rep. 2018 Apr 6;4(4):384-385. doi: 10.1016/j.jdcr.2017.10.013. eCollection 2018 May. No abstract available.


Acrodermatitis acidaemica.

Maguire CA, Chong H, Ramachandran R, Popoola J, Akhras V, Singh M.

Clin Exp Dermatol. 2018 Apr;43(3):315-318. doi: 10.1111/ced.13369. Epub 2018 Jan 15.


Enhanced liver gene transfer and evasion of preexisting humoral immunity with exosome-enveloped AAV vectors.

Meliani A, Boisgerault F, Fitzpatrick Z, Marmier S, Leborgne C, Collaud F, Simon Sola M, Charles S, Ronzitti G, Vignaud A, van Wittenberghe L, Marolleau B, Jouen F, Tan S, Boyer O, Christophe O, Brisson AR, Maguire CA, Mingozzi F.

Blood Adv. 2017 Oct 16;1(23):2019-2031. doi: 10.1182/bloodadvances.2017010181. eCollection 2017 Oct 24.


Extracellular vesicles: nature's nanoparticles for improving gene transfer with adeno-associated virus vectors.

György B, Maguire CA.

Wiley Interdiscip Rev Nanomed Nanobiotechnol. 2018 May;10(3):e1488. doi: 10.1002/wnan.1488. Epub 2017 Aug 11. Review.


Altered circadian feeding behavior and improvement of metabolic syndrome in obese Tac1-deficient mice.

Maguire CA, León S, Carroll RS, Kaiser UB, Navarro VM.

Int J Obes (Lond). 2017 Dec;41(12):1798-1804. doi: 10.1038/ijo.2017.185. Epub 2017 Aug 4.


Tac1 Signaling Is Required for Sexual Maturation and Responsiveness of GnRH Neurons to Kisspeptin in the Male Mouse.

Maguire CA, Song YB, Wu M, León S, Carroll RS, Alreja M, Kaiser UB, Navarro VM.

Endocrinology. 2017 Jul 1;158(7):2319-2329. doi: 10.1210/en.2016-1807.


Histological Features of Methylene Blue-Induced Phototoxicity Administered in the Context of Parathyroid Surgery.

Maguire CA, Sharma A, Alarcon L, Ffolkes L, Kurzepa M, Ostlere L, Samarasinghe V, Singh M.

Am J Dermatopathol. 2017 Aug;39(8):e110-e115. doi: 10.1097/DAD.0000000000000856.


Exosome-associated AAV2 vector mediates robust gene delivery into the murine retina upon intravitreal injection.

Wassmer SJ, Carvalho LS, György B, Vandenberghe LH, Maguire CA.

Sci Rep. 2017 Mar 31;7:45329. doi: 10.1038/srep45329.


Rescue of Hearing by Gene Delivery to Inner-Ear Hair Cells Using Exosome-Associated AAV.

György B, Sage C, Indzhykulian AA, Scheffer DI, Brisson AR, Tan S, Wu X, Volak A, Mu D, Tamvakologos PI, Li Y, Fitzpatrick Z, Ericsson M, Breakefield XO, Corey DP, Maguire CA.

Mol Ther. 2017 Feb 1;25(2):379-391. doi: 10.1016/j.ymthe.2016.12.010. Epub 2017 Jan 9.


Tailored transgene expression to specific cell types in the central nervous system after peripheral injection with AAV9.

Dashkoff J, Lerner EP, Truong N, Klickstein JA, Fan Z, Mu D, Maguire CA, Hyman BT, Hudry E.

Mol Ther Methods Clin Dev. 2016 Dec 7;3:16081. eCollection 2016.


Exosome-associated AAV vector as a robust and convenient neuroscience tool.

Hudry E, Martin C, Gandhi S, György B, Scheffer DI, Mu D, Merkel SF, Mingozzi F, Fitzpatrick Z, Dimant H, Masek M, Ragan T, Tan S, Brisson AR, Ramirez SH, Hyman BT, Maguire CA.

Gene Ther. 2016 Nov;23(11):819. doi: 10.1038/gt.2016.65. No abstract available.


Trafficking of adeno-associated virus vectors across a model of the blood-brain barrier; a comparative study of transcytosis and transduction using primary human brain endothelial cells.

Merkel SF, Andrews AM, Lutton EM, Mu D, Hudry E, Hyman BT, Maguire CA, Ramirez SH.

J Neurochem. 2017 Jan;140(2):216-230. doi: 10.1111/jnc.13861. Epub 2016 Dec 15.


Systemically administered AAV9-sTRAIL combats invasive glioblastoma in a patient-derived orthotopic xenograft model.

Crommentuijn MH, Kantar R, Noske DP, Vandertop WP, Badr CE, Würdinger T, Maguire CA, Tannous BA.

Mol Ther Oncolytics. 2016 Jun 22;3:16017. doi: 10.1038/mto.2016.17. eCollection 2016.


In Vivo Selection Yields AAV-B1 Capsid for Central Nervous System and Muscle Gene Therapy.

Choudhury SR, Fitzpatrick Z, Harris AF, Maitland SA, Ferreira JS, Zhang Y, Ma S, Sharma RB, Gray-Edwards HL, Johnson JA, Johnson AK, Alonso LC, Punzo C, Wagner KR, Maguire CA, Kotin RM, Martin DR, Sena-Esteves M.

Mol Ther. 2016 Aug;24(7):1247-57. doi: 10.1038/mt.2016.84. Epub 2016 Apr 27.

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