Adeno-associated virus vectors for gene therapy of cystic fibrosis

Methods Enzymol. 1998:292:717-32. doi: 10.1016/s0076-6879(98)92055-9.
No abstract available

MeSH terms

  • Adenoviruses, Human / genetics
  • Animals
  • Cystic Fibrosis / physiopathology*
  • Cystic Fibrosis / therapy*
  • Cystic Fibrosis Transmembrane Conductance Regulator / biosynthesis*
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics
  • Dependovirus / genetics*
  • Epithelial Cells / physiology*
  • Gene Transfer Techniques*
  • Genetic Therapy / methods*
  • Genetic Vectors*
  • Humans
  • Lung / physiology*
  • Lung / physiopathology
  • Mice
  • Moloney murine leukemia virus / genetics
  • Mucous Membrane / physiology
  • Mucous Membrane / physiopathology
  • Polymerase Chain Reaction / methods

Substances

  • CFTR protein, human
  • Cystic Fibrosis Transmembrane Conductance Regulator