No abstract available
Publication types
-
Interview
-
Research Support, Non-U.S. Gov't
MeSH terms
-
Clinical Trials as Topic
-
Drug Design
-
Exons
-
Genetic Therapy / methods
-
Humans
-
Muscular Dystrophy, Duchenne / drug therapy*
-
Muscular Dystrophy, Duchenne / genetics*
-
Mutation
-
Oligonucleotides, Antisense / genetics
-
Oligonucleotides, Antisense / pharmacology*
-
Oligonucleotides, Antisense / therapeutic use*
Substances
-
Oligonucleotides, Antisense