Exon skipping, a therapy for Duchenne muscular dystrophy. Interview by Guenter Scheuerbrandt

Acta Myol. 2008 Oct:27:69-73.
No abstract available

Publication types

  • Interview
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Clinical Trials as Topic
  • Drug Design
  • Exons
  • Genetic Therapy / methods
  • Humans
  • Muscular Dystrophy, Duchenne / drug therapy*
  • Muscular Dystrophy, Duchenne / genetics*
  • Mutation
  • Oligonucleotides, Antisense / genetics
  • Oligonucleotides, Antisense / pharmacology*
  • Oligonucleotides, Antisense / therapeutic use*

Substances

  • Oligonucleotides, Antisense