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GeneReviews® [Internet].
Adam MP, Feldman J, Mirzaa GM, et al., editors.
Seattle (WA): University of Washington, Seattle; 1993-2025.
Top results in this bookTable of Contents
Jasper's Basic Mechanisms of the Epilepsies. 5th edition.
Noebels JL, Avoli M, Rogawski MA, et al., editors.
New York: Oxford University Press; 2024.
Fidanacogene Elaparvovec (Beqvez): CADTH Reimbursement Review: Therapeutic area: Hemophilia B [Internet].
Ottawa (ON): Canadian Agency for Drugs and Technologies in Health; 2024 Jun.
Medical Microbiology. 4th edition.
Baron S, editor.
Galveston (TX): University of Texas Medical Branch at Galveston; 1996.
Holland-Frei Cancer Medicine. 6th edition.
Kufe DW, Pollock RE, Weichselbaum RR, et al., editors.
Hamilton (ON): BC Decker; 2003.
Retroviruses.
Coffin JM, Hughes SH, Varmus HE, editors.
Cold Spring Harbor (NY): Cold Spring Harbor Laboratory Press; 1997.
Big Data and Analytics for Infectious Disease Research, Operations, and Policy: Proceedings of a Workshop.
National Academies of Sciences, Engineering, and Medicine; Health and Medicine Division; Board on Global Health; Forum on Microbial Threats.
Washington (DC): National Academies Press (US); 2016 Dec 8.
Translational Neuroscience: Toward New Therapies [Internet].
Nikolich K, Hyman SE, editors.
Cambridge (MA): MIT Press; 2015.
Etranacogene Dezaparvovec (Hemgenix): Therapeutic area: Hemophilia B: CADTH Reimbursement Review [Internet].
Ottawa (ON): Canadian Agency for Drugs and Technologies in Health; 2024 Sep.
Human Papillomaviruses.
IARC Working Group on the Evaluation of Carcinogenic Risks to Humans.
Lyon (FR): International Agency for Research on Cancer; 1995. (IARC Monographs on the Evaluation of Carcinogenic Risks to Humans, No. 64.)
Oversight and Review of Clinical Gene Transfer Protocols: Assessing the Role of the Recombinant DNA Advisory Committee.
Committee on the Independent Review and Assessment of the Activities of the NIH Recombinant DNA Advisory Committee; Board on Health Sciences Policy; Institute of Medicine; Lenzi RN, Altevogt BM, Gostin LO, editors.
Washington (DC): National Academies Press (US); 2014 Mar 27.
Biodefense in the Age of Synthetic Biology.
National Academies of Sciences, Engineering, and Medicine; Division on Earth and Life Studies; Board on Life Sciences; Board on Chemical Sciences and Technology; Committee on Strategies for Identifying and Addressing Potential Biodefense Vulnerabilities Posed by Synthetic Biology.
Washington (DC): National Academies Press (US); 2018 Jun 19.
Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop.
National Academies of Sciences, Engineering, and Medicine; Health and Medicine Division; Board on Health Sciences Policy; Forum on Neuroscience and Nervous System Disorders; Stroud C, Bain L, editors.
Washington (DC): National Academies Press (US); 2019 Sep 20.
Clinical Review Report: Onasemnogene Abeparvovec (Zolgensma): (Novartis Pharmaceuticals Canada Inc.): Indication: For the treatment of pediatric patients with 5q spinal muscular atrophy (SMA) with bi-allelic mutations in the survival motor neuron 1 (SMN1) gene and: 3 or fewer copies of SMN2 gene; or infantile-onset SMA [Internet].
Ottawa (ON): Canadian Agency for Drugs and Technologies in Health; 2021 May.
Gene therapy for choroideremia using an adeno-associated viral vector encoding Rab escort protein 1: the REGENERATE open-label trial.
Cehajic-Kapetanovic J, Bellini MP, Taylor LJ, et al.; REGENERATE Study Group.
Southampton (UK): National Institute for Health and Care Research; 2024 May. (Efficacy and Mechanism Evaluation, No. 11.09.)
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