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GeneReviews® [Internet].
Adam MP, Feldman J, Mirzaa GM, et al., editors.
Seattle (WA): University of Washington, Seattle; 1993-2025.
Top results in this bookTable of Contents
StatPearls [Internet].
Treasure Island (FL): StatPearls Publishing; 2025 Jan-.
Clinical Review Report: Cerliponase Alfa (Brineura): (Biomarin Pharmaceutical (Canada) Inc.): Indication: For the treatment of neuronal ceroid lipofuscinosis type 2 (CLN2) disease, also known as tripeptidyl peptidase 1 (TPP1) deficiency [Internet].
Ottawa (ON): Canadian Agency for Drugs and Technologies in Health; 2019 Jun.
Jasper's Basic Mechanisms of the Epilepsies. 5th edition.
Noebels JL, Avoli M, Rogawski MA, et al., editors.
New York: Oxford University Press; 2024.
Pharmacoeconomic Review Report: Cerliponase Alfa (Brineura): (BioMarin Pharmaceutical (Canada) Inc.): Indication: For the treatment of neuronal ceroid lipofuscinosis type 2 (CLN2) disease, also known as tripeptidyl peptidase 1 (TPP1) deficiency [Internet].
Madame Curie Bioscience Database [Internet].
Austin (TX): Landes Bioscience; 2000-2013.
Fabry Disease: Perspectives from 5 Years of FOS.
Mehta A, Beck M, Sunder-Plassmann G, editors.
Oxford: Oxford PharmaGenesis; 2006.
Toxicological Profile for Phosphate Ester Flame Retardants.
Atlanta (GA): Agency for Toxic Substances and Disease Registry (US); 2012 Sep.
Jasper's Basic Mechanisms of the Epilepsies [Internet]. 4th edition.
Bethesda (MD): National Center for Biotechnology Information (US); 2012.
Future Research Needs for Hematopoietic Stem-Cell Transplantation in the Pediatric Population: Identification of Future Research Needs From Comparative Effectiveness Review No. 48 [Internet].
Belinson S, Mauger Rothenberg B, Chopra R, et al.
Rockville (MD): Agency for Healthcare Research and Quality (US); 2012 Feb. (Future Research Needs Papers, No. 10.)
The Epilepsies: Seizures, Syndromes and Management.
Panayiotopoulos CP.
Oxfordshire (UK): Bladon Medical Publishing; 2005.
Glucose: Neonatal parenteral nutrition: Evidence review D1.
National Guideline Alliance (UK).
London: National Institute for Health and Care Excellence (NICE); 2020 Feb. (NICE Guideline, No. 154.)
Amino acids: Neonatal parenteral nutrition: Evidence review D2.
Ratio of non-nitrogen energy to nitrogen: Neonatal parenteral nutrition: Evidence review D7.
Ratio of carbohydrates to lipids: Neonatal parenteral nutrition: Evidence review D8.
Lipids: Neonatal parenteral nutrition: Evidence review D3.
WormBook: The Online Review of C. elegans Biology [Internet].
Pasadena (CA): WormBook; 2005-2018.
Toxicological Profile for Hydraulic Fluids.
Atlanta (GA): Agency for Toxic Substances and Disease Registry (US); 1997 Sep.
Toxicological Profile for Carbon Tetrachloride.
Atlanta (GA): Agency for Toxic Substances and Disease Registry (US); 2005 Aug.
CADTH Canadian Drug Expert Committee Recommendation: Cerliponase Alfa (Brineura — Biomarin Pharmaceutical [Canada] Inc.): Indication: For the treatment of neuronal ceroid lipofuscinosis type 2 (CLN2) disease, also known as tripeptidyl peptidase 1 (TPP1) deficiency [Internet].
Ottawa (ON): Canadian Agency for Drugs and Technologies in Health; 2019 May.
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