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Accession: PRJNA513291 ID: 513291

Humans; mice

Adenine base editing in an adult mouse model of tyrosinemia

Genome editing in adult mice to cure tyrosinemia
AccessionPRJNA513291
Data TypeRaw sequence reads
ScopeMultispecies
Grants
  • "Integrating Chemistry and Evolution to Illuminate Biology and Enable Novel Therapeutics" (Grant ID R35 GM118062, National Institute of General Medical Sciences)
  • "Continuous Evolution of Proteins with Novel Therapeutic Potential" (Grant ID R01 EB022376, National Institute of Biomedical Imaging and Bioengineering)
  • "Expanding the Scope of Base Editing" (Grant ID U01 AI142756, National Institute of Allergy and Infectious Diseases Extramural Activities)
  • "Center for Genome Editing and Recording" (Grant ID RM1 HG009490, National Human Genome Research Institute)
  • "CRISPR-based modular therapy for precision medicine" (Grant ID DP2 HL137167, National Heart, Lung, and Blood Institute)
  • "New Approaches to Gene Therapy for Alpha-1 Antitrypsin Deficiency" (Grant ID P01 HL131471, National Heart, Lung, and Blood Institute)
  • "Develop combinatorial non-viral and viral CRISPR delivery for lung diseases" (Grant ID UG3 HL147367, National Heart, Lung, and Blood Institute)
  • "Defining the genetic requirements for maintenance of colorectal cancer" (Grant ID K22 CA181280, National Cancer Institute)
  • "A scalable platform for target validation in GEMM models of gastrointestinal malignancies." (Grant ID R01 CA195787, National Cancer Institute)
  • "Marble Center for Cancer Nanomedicine and a Cancer Center Support (core) Grant" (Grant ID P30-CA14051, NCI)
  • "HHMI investigator" (Grant ID HHMI_Liu_D, Howard Hughes Medical Institute)
  • "Safe Genes" (Grant ID HR0011-17-2-0049, Defense Advanced Research Projects Agency)
  • "American Cancer Society Research Scholars Grant" (Grant ID 129056-RSG-16-093, American Cancer Society)
SubmissionRegistration date: 7-Jan-2019
Broad Institute
RelevanceMedical
Project Data:
Resource NameNumber
of Links
Sequence data
SRA Experiments39
Other datasets
BioSample39
SRA Data Details
ParameterValue
Data volume, Gbases1
Data volume, Mbytes496

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