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Gene therapy for inborn errors of liver metabolism: progress towards clinical applications.

Brunetti-Pierri N.

Ital J Pediatr. 2008 Nov 18;34(1):2.PMID: 19490653 [PubMed - in process]Related articlesFree article

Gene therapy for inborn errors of liver metabolism.

Brunetti-Pierri N, Lee B.

Mol Genet Metab. 2005 Sep-Oct;86(1-2):13-24. Review.PMID: 16154372 [PubMed - indexed for MEDLINE]Related articles

Hepatocyte transplantation for correction of inborn errors of metabolism.

Waelzlein JH, Puppi J, Dhawan A.

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Hepatocyte transplantation for inborn errors of metabolism.

Burlina AB.

J Inherit Metab Dis. 2004;27(3):373-83. Review.PMID: 15190195 [PubMed - indexed for MEDLINE]Related articles

Clinical application of somatic gene therapy in inborn errors of metabolism.

Ledley FD.

J Inherit Metab Dis. 1990;13(4):597-616.PMID: 2122123 [PubMed - indexed for MEDLINE]Related articles

Liver transplantation for non-hepatotoxic inborn errors of metabolism.

Treem WR.

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Liver cell transplantation for the treatment of inborn errors of metabolism.

Meyburg J, Hoffmann GF.

J Inherit Metab Dis. 2008 Apr 4. [Epub ahead of print]PMID: 18392744 [PubMed - as supplied by publisher]Related articles

A 25-year longitudinal analysis of treatment efficacy in inborn errors of metabolism.

Campeau PM, Scriver CR, Mitchell JJ.

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Clinical approach to the diagnoses of inborn errors of metabolism.

Kamboj M.

Pediatr Clin North Am. 2008 Oct;55(5):1113-27, viii. Review.PMID: 18929055 [PubMed - indexed for MEDLINE]Related articles

Stem/progenitor cells in liver injury repair and regeneration.

Zhao Q, Ren H, Zhu D, Han Z.

Biol Cell. 2009 Jul 31;101(10):557-71. Review.PMID: 19642968 [PubMed - indexed for MEDLINE]Related articles

Treatment of inborn errors of metabolism.

Schwartz IV, Souza CF, Giugliani R.

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Progress toward cell-directed therapy for phenylketonuria.

Harding C.

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The primary hyperoxalurias.

Bobrowski AE, Langman CB.

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Biologic solutions for degenerative disk disease.

Fassett DR, Kurd MF, Vaccaro AR.

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Chapter 30 Historical aspects of the major neurological vitamin deficiency disorders: the water-soluble B vitamins.

Lanska DJ.

Handb Clin Neurol. 2009;95:445-76.PMID: 19892133 [PubMed - in process]Related articles

Liver cell transplantation in children.

Meyburg J, Schmidt J, Hoffmann GF.

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Metabolic myopathies: a guide and update for clinicians.

Burr ML, Roos JC, Ostör AJ.

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Liver cell transplantation for Crigler-Najjar syndrome type I: update and perspectives.

Lysy PA, Najimi M, Stephenne X, Bourgois A, Smets F, Sokal EM.

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Targeted approaches for gene therapy and the emergence of engineered meganucleases.

Galetto R, Duchateau P, Pâques F.

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Epilepsy and inborn errors of metabolism in children.

Wolf NI, García-Cazorla A, Hoffmann GF.

J Inherit Metab Dis. 2009 Oct;32(5):609-17. Epub 2009 Jul 31.PMID: 19642011 [PubMed - in process]Related articles