PubMed

Relative persistence of AAV serotype 1 vector genomes in dystrophic muscle.

Pacak CA, Conlon T, Mah CS, Byrne BJ.

Genet Vaccines Ther. 2008 Oct 15;6:14.PMID: 18854054 [PubMed - in process]Related articlesFree article

Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.

Pacak CA, Walter GA, Gaidosh G, Bryant N, Lewis MA, Germain S, Mah CS, Campbell KP, Byrne BJ.

Mol Ther. 2007 Oct;15(10):1775-81. Epub 2007 Jul 24.PMID: 17653106 [PubMed - indexed for MEDLINE]Related articles

Overexpression of Galgt2 reduces dystrophic pathology in the skeletal muscles of alpha sarcoglycan-deficient mice.

Xu R, DeVries S, Camboni M, Martin PT.

Am J Pathol. 2009 Jul;175(1):235-47. Epub 2009 Jun 4.PMID: 19498002 [PubMed - indexed for MEDLINE]Related articles

Delivery of alpha- and beta-sarcoglycan by recombinant adeno-associated virus: efficient rescue of muscle, but differential toxicity.

Dressman D, Araishi K, Imamura M, Sasaoka T, Liu LA, Engvall E, Hoffman EP.

Hum Gene Ther. 2002 Sep 1;13(13):1631-46.PMID: 12228018 [PubMed - indexed for MEDLINE]Related articles

Recombinant adeno-associated virus type 8-mediated extensive therapeutic gene delivery into skeletal muscle of alpha-sarcoglycan-deficient mice.

Nishiyama A, Ampong BN, Ohshima S, Shin JH, Nakai H, Imamura M, Miyagoe-Suzuki Y, Okada T, Takeda S.

Hum Gene Ther. 2008 Jul;19(7):719-30.PMID: 18578595 [PubMed - indexed for MEDLINE]Related articles

Muscles of mice deficient in alpha-sarcoglycan maintain large masses and near control force values throughout the life span.

Consolino CM, Duclos F, Lee J, Williamson RA, Campbell KP, Brooks SV.

Physiol Genomics. 2005 Jul 14;22(2):244-56. Epub 2005 May 10.PMID: 15886330 [PubMed - indexed for MEDLINE]Related articlesFree article

Lack of toxicity of alpha-sarcoglycan overexpression supports clinical gene transfer trial in LGMD2D.

Rodino-Klapac LR, Lee JS, Mulligan RC, Clark KR, Mendell JR.

Neurology. 2008 Jul 22;71(4):240-7. Epub 2008 Jun 4.PMID: 18525034 [PubMed - indexed for MEDLINE]Related articles

Recombinant adeno-associated virus serotype 9 leads to preferential cardiac transduction in vivo.

Pacak CA, Mah CS, Thattaliyath BD, Conlon TJ, Lewis MA, Cloutier DE, Zolotukhin I, Tarantal AF, Byrne BJ.

Circ Res. 2006 Aug 18;99(4):e3-9. Epub 2006 Jul 27.PMID: 16873720 [PubMed - indexed for MEDLINE]Related articlesFree article

Phenotypic correction of alpha-sarcoglycan deficiency by intra-arterial injection of a muscle-specific serotype 1 rAAV vector.

Fougerousse F, Bartoli M, Poupiot J, Arandel L, Durand M, Guerchet N, Gicquel E, Danos O, Richard I.

Mol Ther. 2007 Jan;15(1):53-61.PMID: 17164775 [PubMed - indexed for MEDLINE]Related articles

Limb-girdle muscular dystrophy type 2D gene therapy restores alpha-sarcoglycan and associated proteins.

Mendell JR, Rodino-Klapac LR, Rosales-Quintero X, Kota J, Coley BD, Galloway G, Craenen JM, Lewis S, Malik V, Shilling C, Byrne BJ, Conlon T, Campbell KJ, Bremer WG, Viollet L, Walker CM, Sahenk Z, Clark KR.

Ann Neurol. 2009 Sep;66(3):290-7.PMID: 19798725 [PubMed - indexed for MEDLINE]Related articles

Preclinical characterization of a recombinant adeno-associated virus type 1-pseudotyped vector demonstrates dose-dependent injection site inflammation and dissemination of vector genomes to distant sites.

Flotte TR, Conlon TJ, Poirier A, Campbell-Thompson M, Byrne BJ.

Hum Gene Ther. 2007 Mar;18(3):245-56.PMID: 17376008 [PubMed - indexed for MEDLINE]Related articles

Alternate serotype adenovector provides long-term therapeutic gene expression in the eye.

Hamilton MM, Byrnes GA, Gall JG, Brough DE, King CR, Wei LL.

Mol Vis. 2008;14:2535-46. Epub 2008 Dec 30.PMID: 19122827 [PubMed - indexed for MEDLINE]Related articlesFree article

Transduction efficiency and immune response associated with the administration of AAV8 vector into dog skeletal muscle.

Ohshima S, Shin JH, Yuasa K, Nishiyama A, Kira J, Okada T, Takeda S.

Mol Ther. 2009 Jan;17(1):73-80. Epub 2008 Oct 21.PMID: 18941441 [PubMed - indexed for MEDLINE]Related articles

A common disease-associated missense mutation in alpha-sarcoglycan fails to cause muscular dystrophy in mice.

Kobuke K, Piccolo F, Garringer KW, Moore SA, Sweezer E, Yang B, Campbell KP.

Hum Mol Genet. 2008 May 1;17(9):1201-13. Epub 2008 Feb 5.PMID: 18252746 [PubMed - indexed for MEDLINE]Related articlesFree article

Systemic delivery of AAV8 in utero results in gene expression in diaphragm and limb muscle: treatment implications for muscle disorders.

Koppanati BM, Li J, Xiao X, Clemens PR.

Gene Ther. 2009 Sep;16(9):1130-7. Epub 2009 May 28.PMID: 19474806 [PubMed - in process]Related articlesFree article

Ultrastructure of diaphragm from dystrophic alpha-sarcoglycan-null mice.

Jakubiec-Puka A, Biral D, Krawczyk K, Betto R.

Acta Biochim Pol. 2005;52(2):453-60.PMID: 15990925 [PubMed - indexed for MEDLINE]Related articlesFree article

Mannosidase I inhibition rescues the human alpha-sarcoglycan R77C recurrent mutation.

Bartoli M, Gicquel E, Barrault L, Soheili T, Malissen M, Malissen B, Vincent-Lacaze N, Perez N, Udd B, Danos O, Richard I.

Hum Mol Genet. 2008 May 1;17(9):1214-21. Epub 2008 Feb 5.PMID: 18252745 [PubMed - indexed for MEDLINE]Related articlesFree article

Adeno-associated virus serotype-9 efficiently transduces the retinal outer plexiform layer.

Lei B, Zhang K, Yue Y, Ghosh A, Duan D.

Mol Vis. 2009 Jul 17;15:1374-82.PMID: 19626133 [PubMed - indexed for MEDLINE]Related articlesFree article

Adeno-associated virus vector genomes persist as episomal chromatin in primate muscle.

Penaud-Budloo M, Le Guiner C, Nowrouzi A, Toromanoff A, Chérel Y, Chenuaud P, Schmidt M, von Kalle C, Rolling F, Moullier P, Snyder RO.

J Virol. 2008 Aug;82(16):7875-85. Epub 2008 Jun 4.PMID: 18524821 [PubMed - indexed for MEDLINE]Related articlesFree article

Gene therapy following subretinal AAV5 vector delivery is not affected by a previous intravitreal AAV5 vector administration in the partner eye.

Li W, Kong F, Li X, Dai X, Liu X, Zheng Q, Wu R, Zhou X, Lü F, Chang B, Li Q, Hauswirth WW, Qu J, Pang JJ.

Mol Vis. 2009;15:267-75. Epub 2009 Feb 6.PMID: 19190735 [PubMed - indexed for MEDLINE]Related articlesFree article