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Results: 15

Cited In for PubMed (Select 16085464)


Identification of the galactose binding domain of the adeno-associated virus serotype 9 capsid.

Bell CL, Gurda BL, Van Vliet K, Agbandje-McKenna M, Wilson JM.

J Virol. 2012 Jul;86(13):7326-33. doi: 10.1128/JVI.00448-12. Epub 2012 Apr 18.


Long-term correction of very long-chain acyl-coA dehydrogenase deficiency in mice using AAV9 gene therapy.

Keeler AM, Conlon T, Walter G, Zeng H, Shaffer SA, Dungtao F, Erger K, Cossette T, Tang Q, Mueller C, Flotte TR.

Mol Ther. 2012 Jun;20(6):1131-8. doi: 10.1038/mt.2012.39. Epub 2012 Mar 6.


AAV-based neonatal gene therapy for hemophilia A: long-term correction and avoidance of immune responses in mice.

Hu C, Lipshutz GS.

Gene Ther. 2012 Dec;19(12):1166-76. doi: 10.1038/gt.2011.200. Epub 2012 Jan 12.


Adipose tissue-derived mesenchymal stem cell-based liver gene delivery.

Li H, Zhang B, Lu Y, Jorgensen M, Petersen B, Song S.

J Hepatol. 2011 May;54(5):930-8. doi: 10.1016/j.jhep.2010.07.051. Epub 2010 Nov 3.


RH10 provides superior transgene expression in mice when compared with natural AAV serotypes for neonatal gene therapy.

Hu C, Busuttil RW, Lipshutz GS.

J Gene Med. 2010 Sep;12(9):766-78. doi: 10.1002/jgm.1496.


Adeno-associated virus-mediated correction of a canine model of glycogen storage disease type Ia.

Weinstein DA, Correia CE, Conlon T, Specht A, Verstegen J, Onclin-Verstegen K, Campbell-Thompson M, Dhaliwal G, Mirian L, Cossette H, Falk DJ, Germain S, Clement N, Porvasnik S, Fiske L, Struck M, Ramirez HE, Jordan J, Andrutis K, Chou JY, Byrne BJ, Mah CS.

Hum Gene Ther. 2010 Jul;21(7):903-10. doi: 10.1089/hum.2009.157.


Optimized adeno-associated virus (AAV)-protein phosphatase-5 helper viruses for efficient liver transduction by single-stranded AAV vectors: therapeutic expression of factor IX at reduced vector doses.

Jayandharan GR, Zhong L, Sack BK, Rivers AE, Li M, Li B, Herzog RW, Srivastava A.

Hum Gene Ther. 2010 Mar;21(3):271-83. doi: 10.1089/hum.2009.100.


Sexually dimorphic patterns of episomal rAAV genome persistence in the adult mouse liver and correlation with hepatocellular proliferation.

Dane AP, Cunningham SC, Graf NS, Alexander IE.

Mol Ther. 2009 Sep;17(9):1548-54. doi: 10.1038/mt.2009.139. Epub 2009 Jun 30.


AAV2/8-mediated correction of OTC deficiency is robust in adult but not neonatal Spf(ash) mice.

Cunningham SC, Spinoulas A, Carpenter KH, Wilcken B, Kuchel PW, Alexander IE.

Mol Ther. 2009 Aug;17(8):1340-6. doi: 10.1038/mt.2009.88. Epub 2009 Apr 21.


Normoglycemia alone is insufficient to prevent long-term complications of hepatocellular adenoma in glycogen storage disease type Ib mice.

Yiu WH, Pan CJ, Mead PA, Starost MF, Mansfield BC, Chou JY.

J Hepatol. 2009 Nov;51(5):909-17. doi: 10.1016/j.jhep.2008.11.026. Epub 2009 Feb 5.


Recombinant AAV serotype and capsid mutant comparison for pulmonary gene transfer of alpha-1-antitrypsin using invasive and noninvasive delivery.

Liqun Wang R, McLaughlin T, Cossette T, Tang Q, Foust K, Campbell-Thompson M, Martino A, Cruz P, Loiler S, Mueller C, Flotte TR.

Mol Ther. 2009 Jan;17(1):81-7. doi: 10.1038/mt.2008.217. Epub 2008 Oct 21.


Biochemical correction of short-chain acyl-coenzyme A dehydrogenase deficiency after portal vein injection of rAAV8-SCAD.

Beattie SG, Goetzman E, Conlon T, Germain S, Walter G, Campbell-Thompson M, Matern D, Vockley J, Flotte TR.

Hum Gene Ther. 2008 Jun;19(6):579-88. doi: 10.1089/hum.2007.168.


Gene therapy for type I glycogen storage diseases.

Chou JY, Mansfield BC.

Curr Gene Ther. 2007 Apr;7(2):79-88. Review.


Effects of transient immunosuppression on adenoassociated, virus-mediated, liver-directed gene transfer in rhesus macaques and implications for human gene therapy.

Jiang H, Couto LB, Patarroyo-White S, Liu T, Nagy D, Vargas JA, Zhou S, Scallan CD, Sommer J, Vijay S, Mingozzi F, High KA, Pierce GF.

Blood. 2006 Nov 15;108(10):3321-8. Epub 2006 Jul 25.

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