Display Settings:

Format
Items per page
Sort by

Send to:

Choose Destination

Results: 1 to 20 of 109

1.

Enzyme replacement therapy with laronidase (Aldurazyme(®)) for treating mucopolysaccharidosis type I.

Jameson E, Jones S, Wraith JE.

Cochrane Database Syst Rev. 2013 Nov 21;11:CD009354. doi: 10.1002/14651858.CD009354.pub3. Review.

PMID:
24257962
[PubMed - indexed for MEDLINE]
2.

Enzyme replacement therapy with laronidase (Aldurazyme) for treating mucopolysaccharidosis type I.

Jameson E, Jones S, Wraith JE.

Cochrane Database Syst Rev. 2013 Sep 26;9:CD009354. doi: 10.1002/14651858.CD009354.pub2. Review. Update in: Cochrane Database Syst Rev. 2013;11:CD009354.

PMID:
24085657
[PubMed - indexed for MEDLINE]
3.

Enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II (Hunter syndrome).

da Silva EM, Strufaldi MW, Andriolo RB, Silva LA.

Cochrane Database Syst Rev. 2014 Jan 8;1:CD008185. doi: 10.1002/14651858.CD008185.pub3. Review.

PMID:
24399699
[PubMed - indexed for MEDLINE]
4.

Enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II (Hunter syndrome).

da Silva EM, Strufaldi MW, Andriolo RB, Silva LA.

Cochrane Database Syst Rev. 2011 Nov 9;(11):CD008185. doi: 10.1002/14651858.CD008185.pub2. Review. Update in: Cochrane Database Syst Rev. 2014;1:CD008185.

PMID:
22071845
[PubMed - indexed for MEDLINE]
5.

Enzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5 years: results of a multinational study of recombinant human alpha-L-iduronidase (laronidase).

Wraith JE, Beck M, Lane R, van der Ploeg A, Shapiro E, Xue Y, Kakkis ED, Guffon N.

Pediatrics. 2007 Jul;120(1):e37-46. Epub 2007 Jun 4.

PMID:
17606547
[PubMed - indexed for MEDLINE]
Free Article
6.

Long-term efficacy and safety of laronidase in the treatment of mucopolysaccharidosis I.

Clarke LA, Wraith JE, Beck M, Kolodny EH, Pastores GM, Muenzer J, Rapoport DM, Berger KI, Sidman M, Kakkis ED, Cox GF.

Pediatrics. 2009 Jan;123(1):229-40. doi: 10.1542/peds.2007-3847.

PMID:
19117887
[PubMed - indexed for MEDLINE]
Free Article
7.

Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human alpha-L-iduronidase (laronidase).

Wraith JE, Clarke LA, Beck M, Kolodny EH, Pastores GM, Muenzer J, Rapoport DM, Berger KI, Swiedler SJ, Kakkis ED, Braakman T, Chadbourne E, Walton-Bowen K, Cox GF.

J Pediatr. 2004 May;144(5):581-8.

PMID:
15126990
[PubMed - indexed for MEDLINE]
8.

Laronidase.

[No authors listed]

BioDrugs. 2002;16(4):316-8. Review.

PMID:
12196045
[PubMed - indexed for MEDLINE]
9.

Outcome after three years of laronidase enzyme replacement therapy in a patient with Hurler syndrome.

Thomas JA, Jacobs S, Kierstein J, Van Hove J.

J Inherit Metab Dis. 2006 Dec;29(6):762. Epub 2006 Nov 6.

PMID:
17089217
[PubMed - indexed for MEDLINE]
10.

A dose-optimization trial of laronidase (Aldurazyme) in patients with mucopolysaccharidosis I.

Giugliani R, Rojas VM, Martins AM, Valadares ER, Clarke JT, Góes JE, Kakkis ED, Worden MA, Sidman M, Cox GF.

Mol Genet Metab. 2009 Jan;96(1):13-9. doi: 10.1016/j.ymgme.2008.10.009. Epub 2008 Nov 26.

PMID:
19038563
[PubMed - indexed for MEDLINE]
11.

Laronidase treatment of mucopolysaccharidosis I.

Wraith EJ, Hopwood JJ, Fuller M, Meikle PJ, Brooks DA.

BioDrugs. 2005;19(1):1-7. Review.

PMID:
15691212
[PubMed - indexed for MEDLINE]
12.

Enzyme replacement therapy in mucopolysaccharidosis type I.

Miebach E.

Acta Paediatr Suppl. 2005 Mar;94(447):58-60; discussion 57. Review.

PMID:
15895714
[PubMed - indexed for MEDLINE]
13.

Mucopolysaccharidosis Type I.

Clarke LA, Heppner J.

In: Pagon RA, Adam MP, Ardinger HH, Bird TD, Dolan CR, Fong CT, Smith RJH, Stephens K, editors. GeneReviews® [Internet]. Seattle (WA): University of Washington, Seattle; 1993-2014.
2002 Oct 31 [updated 2011 Jul 21].

PMID:
20301341
[PubMed]
Books & Documents
14.

Enzyme replacement therapy for Anderson-Fabry disease.

El Dib RP, Nascimento P, Pastores GM.

Cochrane Database Syst Rev. 2013 Feb 28;2:CD006663. doi: 10.1002/14651858.CD006663.pub3. Review.

PMID:
23450571
[PubMed - indexed for MEDLINE]
15.

Recombinant growth hormone therapy for cystic fibrosis in children and young adults.

Thaker V, Haagensen AL, Carter B, Fedorowicz Z, Houston BW.

Cochrane Database Syst Rev. 2013 Jun 5;6:CD008901. doi: 10.1002/14651858.CD008901.pub2. Review.

PMID:
23737090
[PubMed - indexed for MEDLINE]
16.

Efficacy of recombinant human alpha-L-iduronidase (laronidase) on restricted range of motion of upper extremities in mucopolysaccharidosis type I patients.

Tylki-Szymanska A, Marucha J, Jurecka A, Syczewska M, Czartoryska B.

J Inherit Metab Dis. 2010 Apr;33(2):151-7. doi: 10.1007/s10545-010-9059-9. Epub 2010 Mar 9.

PMID:
20217237
[PubMed - indexed for MEDLINE]
17.

Cochrane Review: Osmotic and stimulant laxatives for the management of childhood constipation (Review).

Gordon M, Naidoo K, Akobeng AK, Thomas AG.

Evid Based Child Health. 2013 Jan;8(1):57-109. doi: 10.1002/ebch.1893. Review.

PMID:
23878124
[PubMed - indexed for MEDLINE]
18.

Desferrioxamine mesylate for managing transfusional iron overload in people with transfusion-dependent thalassaemia.

Fisher SA, Brunskill SJ, Doree C, Gooding S, Chowdhury O, Roberts DJ.

Cochrane Database Syst Rev. 2013 Aug 21;8:CD004450. doi: 10.1002/14651858.CD004450.pub3. Review.

PMID:
23963793
[PubMed - indexed for MEDLINE]
19.

The first 5 years of clinical experience with laronidase enzyme replacement therapy for mucopolysaccharidosis I.

Wraith JE.

Expert Opin Pharmacother. 2005 Mar;6(3):489-506. Review.

PMID:
15794739
[PubMed - indexed for MEDLINE]
20.

[The development of cognitive functions in children with Hurler phenotype mucopolysaccharidosis type I on enzyme replacement therapy with laronidase].

Biernacka M, Jakubowska-Winecka A, Tylki-Szymańska A.

Pediatr Endocrinol Diabetes Metab. 2010;16(4):249-54. Polish.

PMID:
21447265
[PubMed - indexed for MEDLINE]
Free Article

Display Settings:

Format
Items per page
Sort by

Send to:

Choose Destination

Supplemental Content

Write to the Help Desk