Similar articles for PMID: 24035979

Year	Number of Results
2001	1
2002	2
2003	4
2004	3
2005	4
2006	8
2007	3
2008	3
2009	8
2010	6
2011	8
2012	5
2013	9
2014	5
2015	4
2016	5
2017	4
2018	4
2019	4
2020	9
2021	2
2022	3
2023	2
2024	0

1

Persistence of non-viral vector mediated RPE65 expression: case for viability as a gene transfer therapy for RPE-based diseases.

Koirala A, Conley SM, Makkia R, Liu Z, Cooper MJ, Sparrow JR, Naash MI. Koirala A, et al. J Control Release. 2013 Dec 28;172(3):745-52. doi: 10.1016/j.jconrel.2013.08.299. Epub 2013 Sep 11. J Control Release. 2013. PMID: 24035979 Free PMC article.

2

S/MAR-containing DNA nanoparticles promote persistent RPE gene expression and improvement in RPE65-associated LCA.

Koirala A, Makkia RS, Conley SM, Cooper MJ, Naash MI. Koirala A, et al. Hum Mol Genet. 2013 Apr 15;22(8):1632-42. doi: 10.1093/hmg/ddt013. Epub 2013 Jan 18. Hum Mol Genet. 2013. PMID: 23335596 Free PMC article.

3

Gene therapy following subretinal AAV5 vector delivery is not affected by a previous intravitreal AAV5 vector administration in the partner eye.

Li W, Kong F, Li X, Dai X, Liu X, Zheng Q, Wu R, Zhou X, Lü F, Chang B, Li Q, Hauswirth WW, Qu J, Pang JJ. Li W, et al. Mol Vis. 2009;15:267-75. Epub 2009 Feb 6. Mol Vis. 2009. PMID: 19190735 Free PMC article.

4

Nanoparticle-mediated gene transfer specific to retinal pigment epithelial cells.

Koirala A, Makkia RS, Cooper MJ, Naash MI. Koirala A, et al. Biomaterials. 2011 Dec;32(35):9483-93. doi: 10.1016/j.biomaterials.2011.08.062. Epub 2011 Sep 1. Biomaterials. 2011. PMID: 21885113 Free PMC article.

5

Long-term restoration of rod and cone vision by single dose rAAV-mediated gene transfer to the retina in a canine model of childhood blindness.

Acland GM, Aguirre GD, Bennett J, Aleman TS, Cideciyan AV, Bennicelli J, Dejneka NS, Pearce-Kelling SE, Maguire AM, Palczewski K, Hauswirth WW, Jacobson SG. Acland GM, et al. Mol Ther. 2005 Dec;12(6):1072-82. doi: 10.1016/j.ymthe.2005.08.008. Epub 2005 Oct 14. Mol Ther. 2005. PMID: 16226919 Free PMC article.

6

Gene therapy rescues cone structure and function in the 3-month-old rd12 mouse: a model for midcourse RPE65 leber congenital amaurosis.

Li X, Li W, Dai X, Kong F, Zheng Q, Zhou X, Lü F, Chang B, Rohrer B, Hauswirth WW, Qu J, Pang JJ. Li X, et al. Invest Ophthalmol Vis Sci. 2011 Jan 5;52(1):7-15. doi: 10.1167/iovs.10-6138. Print 2011 Jan. Invest Ophthalmol Vis Sci. 2011. PMID: 21169527 Free PMC article.

7

Episomal maintenance of S/MAR-containing non-viral vectors for RPE-based diseases.

Koirala A, Conley SM, Naash MI. Koirala A, et al. Adv Exp Med Biol. 2014;801:703-9. doi: 10.1007/978-1-4614-3209-8_88. Adv Exp Med Biol. 2014. PMID: 24664761

8

The Status of RPE65 Gene Therapy Trials: Safety and Efficacy.

Pierce EA, Bennett J. Pierce EA, et al. Cold Spring Harb Perspect Med. 2015 Jan 29;5(9):a017285. doi: 10.1101/cshperspect.a017285. Cold Spring Harb Perspect Med. 2015. PMID: 25635059 Free PMC article. Review.

9

Gene therapy restores vision-dependent behavior as well as retinal structure and function in a mouse model of RPE65 Leber congenital amaurosis.

Pang JJ, Chang B, Kumar A, Nusinowitz S, Noorwez SM, Li J, Rani A, Foster TC, Chiodo VA, Doyle T, Li H, Malhotra R, Teusner JT, McDowell JH, Min SH, Li Q, Kaushal S, Hauswirth WW. Pang JJ, et al. Mol Ther. 2006 Mar;13(3):565-72. doi: 10.1016/j.ymthe.2005.09.001. Epub 2005 Oct 11. Mol Ther. 2006. PMID: 16223604 Free article.

10

Lentiviral gene transfer of RPE65 rescues survival and function of cones in a mouse model of Leber congenital amaurosis.

Bemelmans AP, Kostic C, Crippa SV, Hauswirth WW, Lem J, Munier FL, Seeliger MW, Wenzel A, Arsenijevic Y. Bemelmans AP, et al. PLoS Med. 2006 Oct;3(10):e347. doi: 10.1371/journal.pmed.0030347. PLoS Med. 2006. PMID: 17032058 Free PMC article.

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