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Items: 1 to 20 of 128

1.

Preclinical transfusion-dependent humanized mouse model of beta thalassemia major.

Huo Y, McConnell SC, Ryan TM.

Blood. 2009 May 7;113(19):4763-70. doi: 10.1182/blood-2008-12-197012. Epub 2009 Mar 3.

2.

A novel murine model of Cooley anemia and its rescue by lentiviral-mediated human beta-globin gene transfer.

Rivella S, May C, Chadburn A, Rivière I, Sadelain M.

Blood. 2003 Apr 15;101(8):2932-9. Epub 2002 Dec 12.

3.

Humanized mouse models of Cooley's anemia: correct fetal-to-adult hemoglobin switching, disease onset, and disease pathology.

Huo Y, McConnell SC, Liu S, Zhang T, Yang R, Ren J, Ryan TM.

Ann N Y Acad Sci. 2010 Aug;1202:45-51. doi: 10.1111/j.1749-6632.2010.05547.x.

PMID:
20712771
4.

Humanized Mouse Model of Cooley's Anemia.

Huo Y, McConnell SC, Liu SR, Yang R, Zhang TT, Sun CW, Wu LC, Ryan TM.

J Biol Chem. 2009 Feb 20;284(8):4889-96. doi: 10.1074/jbc.M805681200. Epub 2008 Dec 19.

6.

Functional requirements for phenotypic correction of murine beta-thalassemia: implications for human gene therapy.

Persons DA, Allay ER, Sabatino DE, Kelly P, Bodine DM, Nienhuis AW.

Blood. 2001 May 15;97(10):3275-82.

7.

mRNA expression of iron regulatory genes in beta-thalassemia intermedia and beta-thalassemia major mouse models.

Weizer-Stern O, Adamsky K, Amariglio N, Rachmilewitz E, Breda L, Rivella S, Rechavi G.

Am J Hematol. 2006 Jul;81(7):479-83.

8.

Therapeutic levels of fetal hemoglobin in erythroid progeny of β-thalassemic CD34+ cells after lentiviral vector-mediated gene transfer.

Wilber A, Hargrove PW, Kim YS, Riberdy JM, Sankaran VG, Papanikolaou E, Georgomanoli M, Anagnou NP, Orkin SH, Nienhuis AW, Persons DA.

Blood. 2011 Mar 10;117(10):2817-26. doi: 10.1182/blood-2010-08-300723. Epub 2010 Dec 14.

9.

Therapeutic hemoglobin levels after gene transfer in β-thalassemia mice and in hematopoietic cells of β-thalassemia and sickle cells disease patients.

Breda L, Casu C, Gardenghi S, Bianchi N, Cartegni L, Narla M, Yazdanbakhsh K, Musso M, Manwani D, Little J, Gardner LB, Kleinert DA, Prus E, Fibach E, Grady RW, Giardina PJ, Gambari R, Rivella S.

PLoS One. 2012;7(3):e32345. doi: 10.1371/journal.pone.0032345. Epub 2012 Mar 27.

10.

Transfusion suppresses erythropoiesis and increases hepcidin in adult patients with β-thalassemia major: a longitudinal study.

Pasricha SR, Frazer DM, Bowden DK, Anderson GJ.

Blood. 2013 Jul 4;122(1):124-33. doi: 10.1182/blood-2012-12-471441. Epub 2013 May 8.

11.

Modified activin receptor IIB ligand trap mitigates ineffective erythropoiesis and disease complications in murine β-thalassemia.

Suragani RN, Cawley SM, Li R, Wallner S, Alexander MJ, Mulivor AW, Gardenghi S, Rivella S, Grinberg AV, Pearsall RS, Kumar R.

Blood. 2014 Jun 19;123(25):3864-72. doi: 10.1182/blood-2013-06-511238. Epub 2014 May 2.

12.

Successful correction of the human beta-thalassemia major phenotype using a lentiviral vector.

Puthenveetil G, Scholes J, Carbonell D, Qureshi N, Xia P, Zeng L, Li S, Yu Y, Hiti AL, Yee JK, Malik P.

Blood. 2004 Dec 1;104(12):3445-53. Epub 2004 Aug 3.

14.

Improvement of erythropoiesis in beta-thalassemic mice by continuous erythropoietin delivery from muscle.

Bohl D, Bosch A, Cardona A, Salvetti A, Heard JM.

Blood. 2000 May 1;95(9):2793-8.

15.

Human globin knock-in mice complete fetal-to-adult hemoglobin switching in postnatal development.

McConnell SC, Huo Y, Liu S, Ryan TM.

Mol Cell Biol. 2011 Feb;31(4):876-83. doi: 10.1128/MCB.00725-10. Epub 2010 Dec 20.

16.

Hydroxyurea responses and fetal hemoglobin induction in beta-thalassemia/HbE patients' peripheral blood erythroid cell culture.

Watanapokasin R, Sanmund D, Winichagoon P, Muta K, Fucharoen S.

Ann Hematol. 2006 Mar;85(3):164-9. Epub 2006 Jan 3.

PMID:
16389564
17.

A combined approach for β-thalassemia based on gene therapy-mediated adult hemoglobin (HbA) production and fetal hemoglobin (HbF) induction.

Zuccato C, Breda L, Salvatori F, Breveglieri G, Gardenghi S, Bianchi N, Brognara E, Lampronti I, Borgatti M, Rivella S, Gambari R.

Ann Hematol. 2012 Aug;91(8):1201-13. doi: 10.1007/s00277-012-1430-5. Epub 2012 Mar 31.

18.

Phenotypic expression of Hb F in common high Hb F determinants in Thailand: roles of α-thalassemia, 5' δ-globin BCL11A binding region and 3' β-globin enhancer.

Prakobkaew N, Fucharoen S, Fuchareon G, Siriratmanawong N.

Eur J Haematol. 2014 Jan;92(1):73-9. doi: 10.1111/ejh.12201. Epub 2013 Oct 24.

PMID:
24112054
19.

Alpha and beta thalassemia.

Muncie HL Jr, Campbell J.

Am Fam Physician. 2009 Aug 15;80(4):339-44. Review.

20.

Hydroxyurea increases hemoglobin F levels and improves the effectiveness of erythropoiesis in beta-thalassemia/hemoglobin E disease.

Fucharoen S, Siritanaratkul N, Winichagoon P, Chowthaworn J, Siriboon W, Muangsup W, Chaicharoen S, Poolsup N, Chindavijak B, Pootrakul P, Piankijagum A, Schechter AN, Rodgers GP.

Blood. 1996 Feb 1;87(3):887-92.

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