Display Settings:

Format
Items per page
Sort by

Send to:

Choose Destination

Results: 1 to 20 of 98

1.

A new direction for gene therapy: intrathymic T cell-specific lentiviral gene transfer.

Seggewiss R, Dunbar CE.

J Clin Invest. 2005 Aug;115(8):2064-7.

PMID:
16075048
[PubMed - indexed for MEDLINE]
Free PMC Article
2.

In vivo correction of ZAP-70 immunodeficiency by intrathymic gene transfer.

Adjali O, Marodon G, Steinberg M, Mongellaz C, Thomas-Vaslin V, Jacquet C, Taylor N, Klatzmann D.

J Clin Invest. 2005 Aug;115(8):2287-95.

PMID:
16075064
[PubMed - indexed for MEDLINE]
Free PMC Article
3.

Stable and functional lymphoid reconstitution in artemis-deficient mice following lentiviral artemis gene transfer into hematopoietic stem cells.

Benjelloun F, Garrigue A, Demerens-de Chappedelaine C, Soulas-Sprauel P, Malassis-Séris M, Stockholm D, Hauer J, Blondeau J, Rivière J, Lim A, Le Lorc'h M, Romana S, Brousse N, Pâques F, Galy A, Charneau P, Fischer A, de Villartay JP, Cavazzana-Calvo M.

Mol Ther. 2008 Aug;16(8):1490-9. doi: 10.1038/mt.2008.118. Epub 2008 Jun 17.

PMID:
18560421
[PubMed - indexed for MEDLINE]
4.

Immunodeficiencies: injecting some safety into SCID gene therapy?

Candotti F, Roifman C, Puck JM.

Gene Ther. 2006 May;13(9):741-3. No abstract available.

PMID:
18360945
[PubMed - indexed for MEDLINE]
5.

Reconstitution of lymphoid development and function in ZAP-70-deficient mice following gene transfer into bone marrow cells.

Otsu M, Steinberg M, Ferrand C, Merida P, Rebouissou C, Tiberghien P, Taylor N, Candotti F, Noraz N.

Blood. 2002 Aug 15;100(4):1248-56.

PMID:
12149205
[PubMed - indexed for MEDLINE]
Free Article
6.

Intrathymic administration of hematopoietic progenitor cells enhances T cell reconstitution in ZAP-70 severe combined immunodeficiency.

Adjali O, Vicente RR, Ferrand C, Jacquet C, Mongellaz C, Tiberghien P, Chebli K, Zimmermann VS, Taylor N.

Proc Natl Acad Sci U S A. 2005 Sep 20;102(38):13586-91. Epub 2005 Sep 7.

PMID:
16174749
[PubMed - indexed for MEDLINE]
Free PMC Article
7.

Restoration of lymphocyte function in Janus kinase 3-deficient mice by retroviral-mediated gene transfer.

Bunting KD, Sangster MY, Ihle JN, Sorrentino BP.

Nat Med. 1998 Jan;4(1):58-64.

PMID:
9427607
[PubMed - indexed for MEDLINE]
8.

Development of an enhanced B-specific lentiviral vector expressing BTK: a tool for gene therapy of XLA.

Moreau T, Barlogis V, Bardin F, Nunes JA, Calmels B, Chabannon C, Tonnelle C.

Gene Ther. 2008 Jun;15(12):942-52. doi: 10.1038/gt.2008.17. Epub 2008 Mar 6.

PMID:
18323795
[PubMed - indexed for MEDLINE]
9.

Reconstitution of T cell receptor signaling in ZAP-70-deficient cells by retroviral transduction of the ZAP-70 gene.

Taylor N, Bacon KB, Smith S, Jahn T, Kadlecek TA, Uribe L, Kohn DB, Gelfand EW, Weiss A, Weinberg K.

J Exp Med. 1996 Nov 1;184(5):2031-6.

PMID:
8920891
[PubMed - indexed for MEDLINE]
Free PMC Article
10.

In situ transduction of stromal cells and thymocytes upon intrathymic injection of lentiviral vectors.

Marodon G, Klatzmann D.

BMC Immunol. 2004 Aug 19;5:18.

PMID:
15318949
[PubMed - indexed for MEDLINE]
Free PMC Article
11.

Ten years of gene therapy for primary immune deficiencies.

Aiuti A, Roncarolo MG.

Hematology Am Soc Hematol Educ Program. 2009:682-9. doi: 10.1182/asheducation-2009.1.682. Review.

PMID:
20008254
[PubMed - indexed for MEDLINE]
Free Article
12.

A new chance for SCID gene therapy.

Bordignon C.

Nat Med. 1998 Jan;4(1):19-20. No abstract available.

PMID:
9427599
[PubMed - indexed for MEDLINE]
13.

Gene therapy for severe combined immunodeficiencies.

Gaspar HB, Thrasher AJ.

Expert Opin Biol Ther. 2005 Sep;5(9):1175-82. Review.

PMID:
16120048
[PubMed - indexed for MEDLINE]
14.

Unique risk factors for insertional mutagenesis in a mouse model of XSCID gene therapy.

Shou Y, Ma Z, Lu T, Sorrentino BP.

Proc Natl Acad Sci U S A. 2006 Aug 1;103(31):11730-5. Epub 2006 Jul 24.

PMID:
16864781
[PubMed - indexed for MEDLINE]
Free PMC Article
15.

In vivo retroviral gene transfer by direct intrafemoral injection results in correction of the SCID phenotype in Jak3 knock-out animals.

McCauslin CS, Wine J, Cheng L, Klarmann KD, Candotti F, Clausen PA, Spence SE, Keller JR.

Blood. 2003 Aug 1;102(3):843-8. Epub 2003 Apr 10.

PMID:
12689938
[PubMed - indexed for MEDLINE]
Free Article
16.

Integration of retroviral vectors induces minor changes in the transcriptional activity of T cells from ADA-SCID patients treated with gene therapy.

Cassani B, Montini E, Maruggi G, Ambrosi A, Mirolo M, Selleri S, Biral E, Frugnoli I, Hernandez-Trujillo V, Di Serio C, Roncarolo MG, Naldini L, Mavilio F, Aiuti A.

Blood. 2009 Oct 22;114(17):3546-56. doi: 10.1182/blood-2009-02-202085. Epub 2009 Aug 3.

PMID:
19652199
[PubMed - indexed for MEDLINE]
Free Article
17.

Application of HSVtk suicide gene to X-SCID gene therapy: ganciclovir treatment offsets gene corrected X-SCID B cells.

Uchiyama T, Kumaki S, Ishikawa Y, Onodera M, Sato M, Du W, Sasahara Y, Tanaka N, Sugamura K, Tsuchiya S.

Biochem Biophys Res Commun. 2006 Mar 10;341(2):391-8. Epub 2006 Jan 11.

PMID:
16426573
[PubMed - indexed for MEDLINE]
18.
19.

[Gene therapy of severe combined immunodeficiency disease: proof of principle of efficiency and safety issues. Gene therapy, primary immunodeficiencies, retrovirus, lentivirus, genome].

Fischer A, Hacein-Bey-Abina S, Lagresle C, Garrigue A, Cavazana-Calvo M.

Bull Acad Natl Med. 2005 May;189(5):779-85; discussion 786-8. French.

PMID:
16433450
[PubMed - indexed for MEDLINE]
20.

Display Settings:

Format
Items per page
Sort by

Send to:

Choose Destination

Supplemental Content

Write to the Help Desk