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Results: 1 to 20 of 97

1.

Systemic delivery of genes to striated muscles using adeno-associated viral vectors.

Gregorevic P, Blankinship MJ, Allen JM, Crawford RW, Meuse L, Miller DG, Russell DW, Chamberlain JS.

Nat Med. 2004 Aug;10(8):828-34. Epub 2004 Jul 25.

PMID:
15273747
[PubMed - indexed for MEDLINE]
Free PMC Article
2.

Gene delivery goes global.

Thomas CE.

Nat Med. 2004 Aug;10(8):782-3. No abstract available.

PMID:
15286775
[PubMed - indexed for MEDLINE]
3.

CTLA4Ig delivered by high-capacity adenoviral vector induces stable expression of dystrophin in mdx mouse muscle.

Jiang Z, Schiedner G, Gilchrist SC, Kochanek S, Clemens PR.

Gene Ther. 2004 Oct;11(19):1453-61.

PMID:
15269713
[PubMed - indexed for MEDLINE]
4.

Delivery of AAV2/9-microdystrophin genes incorporating helix 1 of the coiled-coil motif in the C-terminal domain of dystrophin improves muscle pathology and restores the level of α1-syntrophin and α-dystrobrevin in skeletal muscles of mdx mice.

Koo T, Malerba A, Athanasopoulos T, Trollet C, Boldrin L, Ferry A, Popplewell L, Foster H, Foster K, Dickson G.

Hum Gene Ther. 2011 Nov;22(11):1379-88. doi: 10.1089/hum.2011.020. Epub 2011 May 25.

PMID:
21453126
[PubMed - indexed for MEDLINE]
Free PMC Article
5.

Novel adeno-associated viral vector delivering the utrophin gene regulator jazz counteracts dystrophic pathology in mdx mice.

Strimpakos G, Corbi N, Pisani C, Di Certo MG, Onori A, Luvisetto S, Severini C, Gabanella F, Monaco L, Mattei E, Passananti C.

J Cell Physiol. 2014 Sep;229(9):1283-91. doi: 10.1002/jcp.24567.

PMID:
24469912
[PubMed - indexed for MEDLINE]
Free Article
6.

Stable micro-dystrophin gene transfer using an integrating adeno-retroviral hybrid vector ameliorates the dystrophic pathology in mdx mouse muscle.

Roberts ML, Wells DJ, Graham IR, Fabb SA, Hill VJ, Duisit G, Yuasa K, Takeda S, Cosset FL, Dickson G.

Hum Mol Genet. 2002 Jul 15;11(15):1719-30.

PMID:
12095914
[PubMed - indexed for MEDLINE]
Free Article
7.

A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy.

Rodino-Klapac LR, Janssen PM, Montgomery CL, Coley BD, Chicoine LG, Clark KR, Mendell JR.

J Transl Med. 2007 Sep 24;5:45.

PMID:
17892583
[PubMed - indexed for MEDLINE]
Free PMC Article
8.

Improvement of the mdx mouse dystrophic phenotype by systemic in utero AAV8 delivery of a minidystrophin gene.

Koppanati BM, Li J, Reay DP, Wang B, Daood M, Zheng H, Xiao X, Watchko JF, Clemens PR.

Gene Ther. 2010 Nov;17(11):1355-62. doi: 10.1038/gt.2010.84. Epub 2010 Jun 10.

PMID:
20535217
[PubMed - indexed for MEDLINE]
Free PMC Article
9.

Long-term benefit of adeno-associated virus/antisense-mediated exon skipping in dystrophic mice.

Denti MA, Incitti T, Sthandier O, Nicoletti C, De Angelis FG, Rizzuto E, Auricchio A, Musarò A, Bozzoni I.

Hum Gene Ther. 2008 Jun;19(6):601-8. doi: 10.1089/hum.2008.012.

PMID:
18500943
[PubMed - indexed for MEDLINE]
10.

Full-length dystrophin gene transfer to the mdx mouse in utero.

Reay DP, Bilbao R, Koppanati BM, Cai L, O'Day TL, Jiang Z, Zheng H, Watchko JF, Clemens PR.

Gene Ther. 2008 Apr;15(7):531-6. doi: 10.1038/gt.2008.8. Epub 2008 Feb 14.

PMID:
18273052
[PubMed - indexed for MEDLINE]
11.

Emergent dilated cardiomyopathy caused by targeted repair of dystrophic skeletal muscle.

Townsend D, Yasuda S, Li S, Chamberlain JS, Metzger JM.

Mol Ther. 2008 May;16(5):832-5. doi: 10.1038/mt.2008.52. Epub 2008 Apr 15.

PMID:
18414480
[PubMed - indexed for MEDLINE]
Free PMC Article
12.

Micro-dystrophin and follistatin co-delivery restores muscle function in aged DMD model.

Rodino-Klapac LR, Janssen PM, Shontz KM, Canan B, Montgomery CL, Griffin D, Heller K, Schmelzer L, Handy C, Clark KR, Sahenk Z, Mendell JR, Kaspar BK.

Hum Mol Genet. 2013 Dec 15;22(24):4929-37. doi: 10.1093/hmg/ddt342. Epub 2013 Jul 17.

PMID:
23863459
[PubMed - indexed for MEDLINE]
Free PMC Article
13.

Adeno-associated virus vector-mediated minidystrophin gene therapy improves dystrophic muscle contractile function in mdx mice.

Watchko J, O'Day T, Wang B, Zhou L, Tang Y, Li J, Xiao X.

Hum Gene Ther. 2002 Aug 10;13(12):1451-60.

PMID:
12215266
[PubMed - indexed for MEDLINE]
14.

Systemic microdystrophin gene delivery improves skeletal muscle structure and function in old dystrophic mdx mice.

Gregorevic P, Blankinship MJ, Allen JM, Chamberlain JS.

Mol Ther. 2008 Apr;16(4):657-64. doi: 10.1038/mt.2008.28. Epub 2008 Mar 4.

PMID:
18334986
[PubMed - indexed for MEDLINE]
Free PMC Article
15.

Systemic administration of micro-dystrophin restores cardiac geometry and prevents dobutamine-induced cardiac pump failure.

Townsend D, Blankinship MJ, Allen JM, Gregorevic P, Chamberlain JS, Metzger JM.

Mol Ther. 2007 Jun;15(6):1086-92. Epub 2007 Apr 17.

PMID:
17440445
[PubMed - indexed for MEDLINE]
16.

Sustained muscle expression of dystrophin from a high-capacity adenoviral vector with systemic gene transfer of T cell costimulatory blockade.

Jiang Z, Schiedner G, van Rooijen N, Liu CC, Kochanek S, Clemens PR.

Mol Ther. 2004 Oct;10(4):688-96.

PMID:
15451453
[PubMed - indexed for MEDLINE]
17.

AAV-mediated overexpression of human α7 integrin leads to histological and functional improvement in dystrophic mice.

Heller KN, Montgomery CL, Janssen PM, Clark KR, Mendell JR, Rodino-Klapac LR.

Mol Ther. 2013 Mar;21(3):520-5. doi: 10.1038/mt.2012.281. Epub 2013 Jan 15.

PMID:
23319059
[PubMed - indexed for MEDLINE]
Free PMC Article
18.

Long-term functional adeno-associated virus-microdystrophin expression in the dystrophic CXMDj dog.

Koo T, Okada T, Athanasopoulos T, Foster H, Takeda S, Dickson G.

J Gene Med. 2011 Sep;13(9):497-506. doi: 10.1002/jgm.1602.

PMID:
22144143
[PubMed - indexed for MEDLINE]
19.

Stable transduction of myogenic cells with lentiviral vectors expressing a minidystrophin.

Li S, Kimura E, Fall BM, Reyes M, Angello JC, Welikson R, Hauschka SD, Chamberlain JS.

Gene Ther. 2005 Jul;12(14):1099-108.

PMID:
15759015
[PubMed - indexed for MEDLINE]
20.

Adeno-associated virus vector-mediated gene transfer into dystrophin-deficient skeletal muscles evokes enhanced immune response against the transgene product.

Yuasa K, Sakamoto M, Miyagoe-Suzuki Y, Tanouchi A, Yamamoto H, Li J, Chamberlain JS, Xiao X, Takeda S.

Gene Ther. 2002 Dec;9(23):1576-88.

PMID:
12424610
[PubMed - indexed for MEDLINE]
Free Article

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