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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
1946 1
1967 1
1969 1
1971 1
1973 1
1974 3
1975 1
1977 1
1978 8
1979 2
1982 2
1983 4
1984 5
1985 5
1986 1
1987 1
1988 7
1989 7
1990 8
1991 6
1992 4
1993 8
1994 5
1995 6
1996 11
1997 6
1998 10
1999 11
2000 14
2001 10
2002 26
2003 20
2004 13
2005 16
2006 21
2007 19
2008 28
2009 36
2010 37
2011 36
2012 57
2013 55
2014 39
2015 65
2016 59
2017 49
2018 54
2019 61
2020 50
2021 60
2022 47
2023 56
2024 32

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967 results

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Page 1
Current Clinical Applications of In Vivo Gene Therapy with AAVs.
Mendell JR, Al-Zaidy SA, Rodino-Klapac LR, Goodspeed K, Gray SJ, Kay CN, Boye SL, Boye SE, George LA, Salabarria S, Corti M, Byrne BJ, Tremblay JP. Mendell JR, et al. Among authors: byrne bj. Mol Ther. 2021 Feb 3;29(2):464-488. doi: 10.1016/j.ymthe.2020.12.007. Epub 2020 Dec 10. Mol Ther. 2021. PMID: 33309881 Free PMC article. Review.
Dermato-oncology.
Hegazy S, Byrne B, Raulli G, Dhonncha EN. Hegazy S, et al. Among authors: byrne b. Clin Exp Dermatol. 2024 Mar 21;49(4):416-417. doi: 10.1093/ced/llad404. Clin Exp Dermatol. 2024. PMID: 38011611 No abstract available.
Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy.
Birch SM, Lawlor MW, Conlon TJ, Guo LJ, Crudele JM, Hawkins EC, Nghiem PP, Ahn M, Meng H, Beatka MJ, Fickau BA, Prieto JC, Styner MA, Struharik MJ, Shanks C, Brown KJ, Golebiowski D, Bettis AK, Balog-Alvarez CJ, Clement N, Coleman KE, Corti M, Pan X, Hauschka SD, Gonzalez JP, Morris CA, Schneider JS, Duan D, Chamberlain JS, Byrne BJ, Kornegay JN. Birch SM, et al. Among authors: byrne bj. Sci Transl Med. 2023 Jan 4;15(677):eabo1815. doi: 10.1126/scitranslmed.abo1815. Epub 2023 Jan 4. Sci Transl Med. 2023. PMID: 36599002
Safety and efficacy of cipaglucosidase alfa plus miglustat versus alglucosidase alfa plus placebo in late-onset Pompe disease (PROPEL): an international, randomised, double-blind, parallel-group, phase 3 trial.
Schoser B, Roberts M, Byrne BJ, Sitaraman S, Jiang H, Laforêt P, Toscano A, Castelli J, Díaz-Manera J, Goldman M, van der Ploeg AT, Bratkovic D, Kuchipudi S, Mozaffar T, Kishnani PS; PROPEL Study Group. Schoser B, et al. Among authors: byrne bj. Lancet Neurol. 2021 Dec;20(12):1027-1037. doi: 10.1016/S1474-4422(21)00331-8. Lancet Neurol. 2021. PMID: 34800400 Clinical Trial.
Nicholas Muzyczka, PhD.
Berns KI, Byrne BJ, Flotte TR, Samulski RJ, Srivastava A. Berns KI, et al. Among authors: byrne bj. Mol Ther. 2023 Mar 1;31(3):607. doi: 10.1016/j.ymthe.2023.01.027. Epub 2023 Feb 10. Mol Ther. 2023. PMID: 36764298 Free PMC article. No abstract available.
Current avenues of gene therapy in Pompe disease.
Leon-Astudillo C, Trivedi PD, Sun RC, Gentry MS, Fuller DD, Byrne BJ, Corti M. Leon-Astudillo C, et al. Among authors: byrne bj. Curr Opin Neurol. 2023 Oct 1;36(5):464-473. doi: 10.1097/WCO.0000000000001187. Epub 2023 Jul 19. Curr Opin Neurol. 2023. PMID: 37639402 Review.
967 results