Tissue specific promoters improve specificity of AAV9 mediated transgene expression following intra-vascular gene delivery in neonatal mice.
Pacak CA, Sakai Y, Thattaliyath BD, Mah CS, Byrne BJ.
Genet Vaccines Ther. 2008 Sep 23; 6:13. Epub 2008 Sep 23.
[Genet Vaccines Ther. 2008]