My NCBISign In

Display Settings:

Format

Send to:

Choose Destination
    Rev Med Suisse. 2009 Jan 14;5(186):118-23.

    [Gene therapy for hereditary eye diseases: where are we?].

    [Article in French]
    Viet Tran H, Schorderet DF, Kostic C, Munier FL, Arsenijevic Y.

    Source

    Unité de phénotypage et thérapie moléculaire, Hôpital ophtalmique universitaire Jules-Gonin, 1004 Lausanne. h.tran@ucl.ac.uk

    Abstract

    Recently, preliminary results of three clinical gene therapy trials for early onset retinitis pigmentosa--Leber congenital amaurosis--suggested that treating this degenerative retinal disease by gene transfection can be safe and efficient to restore a visual function. The definitive validation of this therapeutic approach depends on the long-term results. The forthcoming availability of gene therapy in ophthalmology prompts the implementation: of 1) recruitment, 2) phenotyping and genotyping of affected patients, 3) and creation of a hereditary retinopathy registry.

    PMID:
    19238930
    [PubMed - indexed for MEDLINE]

    Publication Types, MeSH Terms

    Publication Types

    MeSH Terms

    LinkOut - more resources

    Medical

      Supplemental Content

      Related citations

      See reviews... See all...

      Recent activity

      Clear Turn Off Turn On

      Your browsing activity is empty.

      Activity recording is turned off.

      Turn recording back on

      See more...
      You are here: NCBI > Literature > PubMed
      Write to the Help Desk