University of Missouri, Department of Molecular Microbiology and Immunology, M610 Medical Sciences Building, One Hospital Drive, Columbia, MO 65212, USA. duand@missouri.edu
Transgene SA is developing Myodys, a non-viral plasmid gene therapy for the potential treatment of Duchenne muscular dystrophy and Becker muscular dystrophy. Phase I clinical trials have been completed, and a phase II clinical trial is planned.