Division of Neurogenetics, Kennedy Krieger Institute, Departments of Neurology, Johns Hopkins University, USA. moser@kennedykrieger.org
PMID: 15139299 [PubMed - indexed for MEDLINE]
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[J Inherit Metab Dis. 2000]
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[Curr Opin Mol Ther. 2008]
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[Minerva Pediatr. 1991]
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[Pediatr Transplant. 2005]
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