Hum Gene Ther. 2000 Mar 20;11(5):777-90.
Phase I clinical trial utilizing gene therapy for limb girdle muscular dystrophy: alpha-, beta-, gamma-, or delta-sarcoglycan gene delivered with intramuscular instillations of adeno-associated vectors.
Stedman H, Wilson JM, Finke R, Kleckner AL, Mendell J.
University of Pennsylvania Health System, Institute for Human Gene Therapy, Philadelphia 19104, USA.
PMID: 10757357 [PubMed - indexed for MEDLINE]
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